Therapeutic antisense oligonucleotide mitigates retinal dysfunction in a pig model of CLN3 Batten disease
治疗性反义寡核苷酸可减轻CLN3巴顿病猪模型中的视网膜功能障碍
期刊:Nucleic Acids Research
影响因子:13.1
doi:10.1093/nar/gkaf1141
Stratton, Matthew P; Centa, Jessica L; Swier, Vicki J; Pfeifer, Wanda L; Booth, Clarissa D; Albert, Karlee; Hunyara, John L; Rechtzigel, Mitchell J; Duelli, Fox J; Leppert, Hannah G; Rigo, Frank; Smit, Trisha; Jafar-Nejad, Paymaan; Weimer, Jill M; Drack, Arlene V; Hastings, Michelle L
