Safety and efficacy of deoxycytidine/deoxythymidine combination therapy in POLG-related disorders: 6-month interim results of an open-label, single arm, phase 2 trial
脱氧胞苷/脱氧胸苷联合疗法治疗POLG相关疾病的安全性和有效性：一项开放标签、单臂II期试验的6个月中期结果
期刊:EClinicalMedicine
影响因子:10
doi:10.1016/j.eclinm.2024.102740
Pekeles, Heather; Berrahmoune, Saoussen; Dassi, Christelle; Cheung, Anthony C T; Gagnon, Tommy; Waters, Paula J; Eberhard, Ralf; Buhas, Daniela; Myers, Kenneth A
