日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Pharmacological inhibition of sclerostin protects bone from B-cell acute lymphoblastic leukemia-mediated destruction

药物抑制硬骨蛋白可保护骨骼免受B细胞急性淋巴细胞白血病介导的破坏。

Kuek, Vincent; Oommen, Joyce; Ferrari, Emanuela; Yuan, Jinbo; Economides, Aris N; Lock, Richard B; Malinge, Sebastien; Kotecha, Rishi S; Cheung, Laurence C

Pharmacological inhibition of sclerostin protects bone from B‐cell acute lymphoblastic leukemia‐mediated destruction

药物抑制硬骨蛋白可保护骨骼免受B细胞急性淋巴细胞白血病介导的破坏。

Anargyrou, Konstantinos; Fotiou, Despina; Vassilakopoulos, Theodoros P; Christoulas, Dimitrios; Makras, Polyzois; Dimou, Maria; Ntanasis-Stathopoulos, Ioannis; Masouridou, Stavroula; Angelopoulou, Maria K; Papatheodorou, Athanasios; Tsionos, Konstantinos; Panayiotidis, Panayiotis; Dimopoulos, Meletios A; Terpos, Evangelos; Kuek, Vincent; Oommen, Joyce; Ferrari, Emanuela; Yuan, Jinbo; Economides, Aris N; Lock, Richard B; Malinge, Sebastien; Kotecha, Rishi S; Cheung, Laurence C

Germline-targeted baboon apolipoprotein L-1 protects mice against African trypanosomes

生殖系靶向狒狒载脂蛋白L-1可保护小鼠免受非洲锥虫感染

Fresard, Sara; Pangburn, Sarah J; Leiss, Kayla; Boodwa-Ko, Daphne; Kovacsics, Daniella; Schoenherr, Chris J; Rabinowitz, Jeremy S; Economides, Aris N; Li, Li; Qiu, Weigang; Gonzalez-Baradat, Bernardo; Rosa, Alessandro; Thomson, Russell; Raper, Jayne; Verdi, Joseph

CryoEM structure of ALK2:BMP6 reveals distinct mechanism that allow ALK2 to interact with both BMP and activin ligands

ALK2:BMP6 的冷冻电镜结构揭示了 ALK2 与 BMP 和激活素配体相互作用的独特机制

Goebel, Erich J; Aykul, Senem; Hom, Warren W; Saotome, Kei; Economides, Aris N; Franklin, Matthew C; Idone, Vincent J

A rare variant in GPR156 associated with depression in a Mennonite pedigree causes habenula hyperactivity and stress sensitivity in mice

在门诺派家族中发现的一种与抑郁症相关的GPR156罕见变异会导致小鼠缰核过度活跃和应激敏感性。

Miller, Bradley R; Gonzaga-Jauregui, Claudia; Brigatti, Karlla W; de Jong, Job; Breese, Robert S; Ko, Seung Yeon; Puffenberger, Erik G; Van Hout, Cristopher; Young, Millie; Luna, Victor M; Staples, Jeffrey; First, Michael B; Gregoire, Hilledna J; Dwork, Andrew J; Pefanis, Evangelos; McCarthy, Shane; Brydges, Susannah; Rojas, Jose; Ye, Bin; Stahl, Eli; Di Gioia, Silvio Alessandro; Hen, René; Elwood, Kevin; Rosoklija, Gorazd; Li, Dadong; Mellis, Scott; Carey, David; Croll, Susan D; Overton, John D; Macdonald, Lynn E; Economides, Aris N; Shuldiner, Alan R; Chuhma, Nao; Rayport, Stephen; Amin, Najaf; Kushner, Steven A; Alessandri-Haber, Nicole; Markx, Sander; Strauss, Kevin A

A TMPRSS6-inhibiting mAb improves disease in a β-thalassemia mouse model and reduces iron in healthy humans

TMPRSS6抑制剂单克隆抗体可改善β-地中海贫血小鼠模型中的疾病症状,并降低健康人体内铁含量。

Lob, Heinrich E; Singh, Nikhil; Mohammadi, Kusha; Ivanova, Larisa; Crowell, Beth; Kim, Hyon J; Kravets, Leah; Das, Nanditha M; Ray, Yonaton; Kim, Jee Hae; Rottey, Sylvie; Labriola-Tompkins, Emily; Hassan, Hazem E; Farrelly, Lorna; Chin, Harvey F; Preda, Marilena; Spencer Noakes, Leigh; Saotome, Kei; Franklin, Matthew; Retter, Marc W; Karayusuf, Elif; Flanagan, John J; Olson, William; Nannuru, Kalyan C; Idone, Vincent; Burczynski, Michael E; Harari, Olivier A; Perlee, Lorah; Van Lancker, Griet; Murphy, Andrew J; Economides, Aris N; Hatsell, Sarah J

Functional, sustained recovery of hearing in Otoferlin-deficient mice using DB-OTO, a hair-cell-specific AAV-based gene therapy.

使用 DB-OTO(一种基于 AAV 的毛细胞特异性基因疗法)使 Otoferlin 缺陷小鼠的听力得到功能性、持续性恢复。

Chung Yoojin, Koehler Seth D, Cancelarich Sarah, Gibson Tyler M, Pregernig Gabriela, Becker Lars, Artinian Quynh-Anh, Goodliffe Joseph W, Pan Ning, Quigley Tera M, Senapati Arun, Slade Peter G, Smith Lillian M, So Kathy S, Zhang Xichun, Corrales C Eduardo, Weber Peter, Macdonald Lynn E, Zambrowicz Brian, Economides Aris N, Kyratsous Christos A, Burns Joseph C, Palermo Adam T, Sabin Leah R, Lee John, Valayannopoulos Vassili, Whitton Jonathon P, Drummond Meghan C

Characterization of flare-ups and impact of garetosmab in adults with fibrodysplasia ossificans progressiva: a post hoc analysis of the randomized, double-blind, placebo-controlled LUMINA-1 trial

对进行性骨化性纤维发育不良成人患者病情加重及garetosmab疗效的描述:一项随机、双盲、安慰剂对照LUMINA-1试验的事后分析

Keen, Richard; Dahir, Kathryn M; McGinniss, Jennifer; Sanchez, Robert J; Mellis, Scott; Economides, Aris N; Di Rocco, Maja; Orcel, Philippe; Roux, Christian; Tabarkiewicz, Jacek; Bachiller-Corral, Javier; Cheung, Angela M; Al Mukaddam, Mona; Mohammadi, Kusha; Gu, Jing; Srinivasan, Dushyanth; Trotter, Dinko Gonzalez; Eekhoff, E Marelise W; Kaplan, Frederick S; Pignolo, Robert J

How Activin A Became a Therapeutic Target in Fibrodysplasia Ossificans Progressiva

Activin A 如何成为进行性骨化性纤维发育不良的治疗靶点

Srinivasan, Dushyanth; Arostegui, Martin; Goebel, Erich J; Hart, Kaitlin N; Aykul, Senem; Lees-Shepard, John B; Idone, Vincent; Hatsell, Sarah J; Economides, Aris N

Garetosmab in fibrodysplasia ossificans progressiva: a randomized, double-blind, placebo-controlled phase 2 trial

Garetosmab治疗进行性骨化性纤维发育不良:一项随机、双盲、安慰剂对照的II期试验

Di Rocco, Maja; Forleo-Neto, Eduardo; Pignolo, Robert J; Keen, Richard; Orcel, Philippe; Funck-Brentano, Thomas; Roux, Christian; Kolta, Sami; Madeo, Annalisa; Bubbear, Judith S; Tabarkiewicz, Jacek; Szczepanek, Małgorzata; Bachiller-Corral, Javier; Cheung, Angela M; Dahir, Kathryn M; Botman, Esmée; Raijmakers, Pieter G; Al Mukaddam, Mona; Tile, Lianne; Portal-Celhay, Cynthia; Sarkar, Neena; Hou, Peijie; Musser, Bret J; Boyapati, Anita; Mohammadi, Kusha; Mellis, Scott J; Rankin, Andrew J; Economides, Aris N; Trotter, Dinko Gonzalez; Herman, Gary A; O'Meara, Sarah J; DelGizzi, Richard; Weinreich, David M; Yancopoulos, George D; Eekhoff, E Marelise W; Kaplan, Frederick S