Semi-automated workflows to quantify AAV transduction in various brain areas and predict gene editing outcome for neurological disorders
半自动化工作流程可量化大脑各个区域的 AAV 转导并预测神经系统疾病的基因编辑结果
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1016/j.omtm.2023.03.013
Fábio Duarte, Mergim Ramosaj, Ed Hasanovic, Sara Regio, Melanie Sipion, Maria Rey, Nicole Déglon