Quantifying the impact of symptomatic acute hepatic porphyria on well-being via patient-reported outcomes: Results from the Porphyria Worldwide Patient Experience Research (POWER) study
通过患者报告结局量化症状性急性肝卟啉症对患者福祉的影响:来自全球卟啉症患者体验研究 (POWER) 的结果
期刊:JIMD Reports
影响因子:1.8
doi:10.1002/jmd2.12343
Dickey, Amy; Wheeden, Kristen; Lyon, Desiree; Burrell, Sue; Hegarty, Sean; Falchetto, Rocco; Williams, Edrin R; Barman-Aksözen, Jasmin; DeCongelio, Marc; Bulkley, Alison; Matos, Joana E; Mnif, Tarek; Mora, Jordanna; Ko, John J; Meninger, Stephen; Lombardelli, Stephen; Nance, Danielle