日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Hematopoietic Stem-Cell Gene Therapy for Cystinosis

胱氨酸病的造血干细胞基因治疗

Barshop, Bruce A; Ball, Edward D; Benador, Nadine; Trauner, Doris; Phillips, Susan; Dohil, Ranjan; Afshari, Natalie A; Roy, Sohini; Campo Fernandes, Beatriz; Kohn, Donald; Shayan, Katayoon; Everett, John K; Bushman, Frederic D; Midgley, Julian; Liang, Hong; Sawyers, Anne; Gangoiti, Jon A; Panchal, Maulik; Ahmed, Imama; Cherqui, Stephanie

Polyclonal origins of human premalignant colorectal lesions

人类结直肠癌前病变的多克隆起源

Van Egeren, Debra; Schenck, Ryan O; Khan, Aziz; Horning, Aaron M; Mo, Shanlan; Weiß, Clemens L; Esplin, Edward D; Becker, Winston R; Wu, Si; Hanson, Casey; Barapour, Nasim; Jiang, Lihua; Contrepois, Kévin; Lee, Hayan; Nevins, Stephanie A; Guha, Tuhin K; Zhang, Hao; He, Zhen; Ma, Zhicheng; Monte, Emma; Karathanos, Thomas V; Laquindanum, Rozelle; Mills, Meredith A; Chaib, Hassan; Chiu, Roxanne; Jian, Ruiqi; Chan, Joanne; Ellenberger, Mathew; Bahmani, Bahareh; Michael, Basil; Weimer, Annika K; Esplin, D Glen; Lancaster, Samuel; Shen, Jeanne; Ladabaum, Uri; Longacre, Teri A; Kundaje, Anshul; Greenleaf, William J; Hu, Zheng; Ford, James M; Snyder, Michael P; Curtis, Christina

The proteostasis network is a therapeutic target in acute myeloid leukemia

蛋白质稳态网络是急性髓系白血病的一个治疗靶点。

Lam, Kentson; Kim, Yoon Joon; Tan, Evelyn L; Ong, Carlo M; Liu, Andrea Z; Zhou, Fanny J; Sunshine, Mary Jean; Chua, Bernadette A; Vicenzi, Silvia; Chen, Katelyn; Yu, Helena; Ford, Pierce W; Zhou, Jie-Hua; Hong, Yuning; Bennett, Eric J; Crews, Leslie A; Ball, Edward D; Signer, Robert A J

The Yeh pilus adhesin is equipped with an α-helical flap motif, which contributes to pectin adherence

叶菌毛粘附素具有α螺旋瓣状结构,有助于果胶粘附。

Kevin O Tamadonfar,Roger D Klein,Edward D B Lopatto,Maxwell I Zimmerman,Philippe N Azimzadeh,Denise A Sanick,Justin R Porter,Jesus Bazan Villicana,Jerome S Pinkner,Bo Huey Chiang,Nathaniel C Gualberto,Karen W Dodson,Michael L Patnode,George M H Birchenough,Gregory R Bowman,Scott J Hultgren

Identification of tofersen PD-response biomarkers in VALOR clinical trial CSF via multiplexed quantitative proteomics.

通过多重定量蛋白质组学鉴定 VALOR 临床试验脑脊液中托福生帕金森反应生物标志物。

Guise Amanda J, Ferber Kyle L, Young Damon, Edwards Amanda L, Sabouri Somayeh, Fraser Kyle B, Milliman Eric, Plowey Edward D, Zoghbi Jad, Fradette Stephanie M, Graham Danielle L

Effect of Cognitive Reserve on Age at Symptom Onset and Cognitive Decline in Individuals With Dominantly Inherited Alzheimer Disease

认知储备对显性遗传阿尔茨海默病患者症状出现年龄和认知衰退的影响

Llibre-Guerra, Jorge J; Lu, Ruijin; Clarens, Ma Florencia; Liu, Ian; Renton, Alan; Ryan, Natalie S; Goate, Alison M; Aguillón, David; Allegri, Ricardo Francisco; Benzinger, Tammie L S; Berman, Sarah; Chhatwal, Jasmeer P; Chrem Mendez, Patricio; Vigo, Gabriela; Cruchaga, Carlos; Day, Gregory S; Farlow, Martin R; Fox, Nick C; Gordon, Brian Andrew; Hassenstab, Jason; Huey, Edward D; Ibanez, Laura; Ikeuchi, Takeshi; Jucker, Mathias; Lee, Jae-Hong; Levey, Allan I; Levin, Johannes; Niimi, Yoshiki; Perrin, Richard J; Rosa-Neto, Pedro; Sánchez-Valle, Raquel; Schofield, Peter R; Wang, Guoqiao; Li, Yan; Xiong, Chengjie; Morris, John C; Karch, Celeste; Daniels, Alisha J; McDade, Eric; Bateman, Randall J

The Electronic Medical Records and Genomics study: Design and analytic framework for assessing the impact of genome-informed risk assessments

电子病历与基因组学研究:评估基因组信息风险评估影响的设计和分析框架

Limdi, Nita; Beasley, T Mark; Cortopassi, Josh; Davis, Brittney; Bangash, Hana; Chen, Jingheng; Chisholm, Rex L; Chung, Wendy K; Cimino, James J; Connolly, John; Crosslin, David R; Davis, Kyle W; DiVietro, Alanna; Esplin, Edward D; Freimuth, Bob; Gordon, Adam; Hakonarson, Hakon; Hamed, Marwan; He, Megan; Hoell, Christin; Holm, Ingrid; Hripscak, George; Irvin, Margurite R; Jarvik, Gail P; Karavite, Dean; Karlson, Elizabeth W; Kenny, Eimear E; Khan, Atlas; Kiryluk, Krzysztof; Knerr, Sarah; Korf, Bruce; Kottyan, Leah; Kullo, Iftikhar; Larkin, Katie; Lennon, Niall; Linder, Jodell E; Manolio, Teri; Martin, Lisa J; McNally, Elizabeth M; Morse, Jennifer; Murphy, Shawn; Namjou, Bahram; Odgis, Jacqueline A; Orlando, Lori; Pacheco, Jennifer; Peterson, Josh F; Pineda-Alvarez, Daniel E; Prows, Cindy; Puckelwartz, Megan; Purcell, Jasmine; Rasmussen-Torvik, Laura; Rehm, Heidi; Roden, Dan M; Rosenthal, Elisabeth A; Rowley, Robb; Sabatello, Maya; Schaid, Daniel; Sharp, Richard; Smith, Johanna L; Smoller, Jordan W; Soper, Emily R; Sterling, Rene; Suckiel, Sabrina A; Terek, Shannon; Thayer, Jeritt; Ting, Yi-Lee; Tiwari, Hemant; Velez-Edwards, Digna; Wagholikar, Kavishwar B; Walunas, Theresa; Wei, Wei-Qi; Weng, Chunua; Wiesner, Georgia; Abul-Husn, Noura S; Veenstra, David L

Potential role of MRI to optimize clinical trial design for progressive supranuclear palsy and corticobasal degeneration

磁共振成像在优化进行性核上性麻痹和皮质基底节变性临床试验设计中的潜在作用

García-Castro, Jesús; VandeVrede, Lawren; Donohue, Michael C; Vaqué-Alcázar, Lídia; Rubio-Guerra, Sara; Selma-González, Judit; Heuer, Hilary W; Morcillo-Nieto, Alejandra O; Franquesa, María; Dols-Icardo, Oriol; Bejanin, Alexandre; Belbin, Olivia; Fortea, Juan; Alcolea, Daniel; Carmona-Iragui, Maria; Abdelnour, Carla; Barroeta, Isabel; Santos-Santos, Miguel; Sánchez Saudinós, María Belen; Sala, Isabel; Lleó, Alberto; Gorno-Tempini, Maria Luisa; Mandelli, Maria Luisa; Raman, Rema; Wills, Anne-Marie A; Barragan, Eden; Litvan, Irene; Boeve, Brad; Dickerson, Brad; Grossman, Murray; Huey, Edward D; Irwin, David J; Pantelyat, Alex; Tartaglia, Carmela; Rojas, Julio C; Boxer, Adam L; Illán-Gala, Ignacio

Machine Learning-Enhanced Clinical Decision Support for Diagnosing Sinusitis With Nasal Endoscopy

利用机器学习增强临床决策支持技术,通过鼻内窥镜诊断鼻窦炎

Gyawali, Dipesh; Mundy, Thomas; Hosseini, Majid; Bodaghi, Morteza; Fujiwara, Akio; Bhatia, Sejal Shyam; Baker, Kayla; Bartolone, Elena; Patel, Dhara; Chu, Henry; Gottumukkala, Raju; Bidwell, Jonathan; McCoul, Edward D

Evaluation of amyloid change as a surrogate for cognitive decline: demonstration in individual-level data from the A4 study of solanezumab

评估淀粉样蛋白变化作为认知能力下降的替代指标:来自solanezumab A4研究的个体水平数据证明

Ackley, Sarah F; Flanders, Michael D; Murchland, Audrey; Chen, Ruijia; Wang, Jingxuan; Shah, Sachin J; Huey, Edward D; Glymour, M Maria