Phase 1/2 trial of brogidirsen: Dual-targeting antisense oligonucleotides for exon 44 skipping in Duchenne muscular dystrophy
brogidirsen 的 1/2 期试验：用于杜氏肌营养不良症外显子 44 跳跃的双靶点反义寡核苷酸
期刊:Cell Reports Medicine
影响因子:11.7
doi:10.1016/j.xcrm.2024.101901
Hirofumi Komaki,Eri Takeshita,Katsuhiko Kunitake,Takami Ishizuka,Yuko Shimizu-Motohashi,Akihiko Ishiyama,Masayuki Sasaki,Chihiro Yonee,Shinsuke Maruyama,Eisuke Hida,Yoshitsugu Aoki
