Toward an all-in-one recombinant adeno-associated virus vector for functionally ablating the prion gene using CRISPR-Cas technology.
利用 CRISPR-Cas 技术构建多功能重组腺相关病毒载体,以功能性地消除朊病毒基因。
期刊:PLoS One
影响因子:2.6
doi:10.1371/journal.pone.0336578
Verkuyl Claire, Belotserkovsky Ari, Zerbes Thomas, Williams Declan, Krishnan Medha R, Zhu Sabrina, GrunnesjÓ§ Sophie, Eid Shehab, Zhang Cunjie, Zhao Wenda, Xu Leo, Lin Eleanore, O'Shea Teaghan, Draper Benjamin, Jungman Andreas, Most Patrick, Schmitt-Ulms Gerold