In vivo CRISPR-Cas9 genome editing in mice identifies genetic modifiers of somatic CAG repeat instability in Huntington's disease
小鼠体内 CRISPR-Cas9 基因组编辑可识别亨廷顿氏病中体细胞 CAG 重复不稳定性基因修饰因子
期刊:Nature Genetics
影响因子:31.7
doi:10.1038/s41588-024-02054-5
Ricardo Mouro Pinto, Ryan Murtha, António Azevedo, Cameron Douglas, Marina Kovalenko, Jessica Ulloa, Steven Crescenti, Zoe Burch, Esaria Oliver, Maheswaran Kesavan, Shota Shibata, Antonia Vitalo, Eduarda Mota-Silva, Marion J Riggs, Kevin Correia, Emanuela Elezi, Brigitte Demelo, Jeffrey B Carroll, T