日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Sustained correction of FVII deficiency in dogs using AAV-mediated expression of zymogen FVII

使用 AAV 介导的酶原 FVII 表达持续纠正狗的 FVII 缺乏症

Oscar A Marcos-Contreras, Shannon M Smith, Dwight A Bellinger, Robin A Raymer, Elizabeth Merricks, Armida Faella, Giulia Pavani, Shangzhen Zhou, Timothy C Nichols, Katherine A High, Paris Margaritis

Circumventing furin enhances factor VIII biological activity and ameliorates bleeding phenotypes in hemophilia models

绕过弗林蛋白酶可增强Ⅷ因子的生物活性并改善血友病模型中的出血表型

Joshua I Siner, Benjamin J Samelson-Jones, Julie M Crudele, Robert A French, Benjamin J Lee, Shanzhen Zhou, Elizabeth Merricks, Robin Raymer, Timothy C Nichols, Rodney M Camire, Valder R Arruda

Platelet-targeted gene therapy with human factor VIII establishes haemostasis in dogs with haemophilia A

利用人类因子 VIII 进行血小板靶向基因治疗可为患有 A 型血友病的犬建立止血

Lily M Du, Paquita Nurden, Alan T Nurden, Timothy C Nichols, Dwight A Bellinger, Eric S Jensen, Sandra L Haberichter, Elizabeth Merricks, Robin A Raymer, Juan Fang, Sevasti B Koukouritaki, Paula M Jacobi, Troy B Hawkins, Kenneth Cornetta, Qizhen Shi, David A Wilcox