日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Lipid nanoparticles and siRNA targeting plasminogen provide lasting inhibition of fibrinolysis in mouse and dog models of hemophilia A

针对纤溶酶原的脂质纳米颗粒和 siRNA 可在小鼠和狗血友病 A 模型中持久抑制纤维蛋白溶解

Amy W Strilchuk, Woosuk S Hur, Paul Batty, Yaqiu Sang, Sara R Abrahams, Alyssa S M Yong, Jerry Leung, Lakmali M Silva, Jocelyn A Schroeder, Kate Nesbitt, Bas de Laat, Niki M Moutsopoulos, Thomas H Bugge, Qizhen Shi, Pieter R Cullis, Elizabeth P Merricks, Alisa S Wolberg, Matthew J Flick, David Lilli

Analysis of vector genome integrations in multicentric lymphoma after AAV gene therapy in a severe hemophilia A dog

重症血友病 A 犬 AAV 基因治疗后多中心淋巴瘤载体基因组整合分析

Lucas Van Gorder, Bhavya S Doshi, Elinor Willis, Timothy C Nichols, Emma Cook, John K Everett, Elizabeth P Merricks, Valder R Arruda, Frederic D Bushman, Mary Beth Callan, Benjamin J Samelson-Jones

Chimeric Mice Engrafted With Canine Hepatocytes Exhibits Similar AAV Transduction Efficiency to Hemophilia B Dog

植入犬肝细胞的嵌合小鼠表现出与血友病 B 犬相似的 AAV 转导效率

Wenwei Shao, Junjiang Sun, Xiaojing Chen, Amanda Dobbins, Elizabeth P Merricks, R Jude Samulski, Timothy C Nichols, Chengwen Li

Dexamethasone Transiently Enhances Transgene Expression in the Liver When Administered at Late-Phase Post Long-Term Adeno-Associated Virus Transduction

腺相关病毒长期转导后后期给予地塞米松可暂时增强肝脏中的转基因表达

Zheng Chai, Xintao Zhang, Amanda Lee Dobbins, Richard Jude Samulski, Elizabeth P Merricks, Timothy C Nichols, Chengwen Li

A long-term study of AAV gene therapy in dogs with hemophilia A identifies clonal expansions of transduced liver cells

对患有血友病 A 的狗进行 AAV 基因治疗的长期研究发现,转导肝细胞出现克隆扩增

Giang N Nguyen #, John K Everett #, Samita Kafle, Aoife M Roche, Hayley E Raymond, Jacob Leiby, Christian Wood, Charles-Antoine Assenmacher, Elizabeth P Merricks, C Tyler Long, Haig H Kazazian, Timothy C Nichols, Frederic D Bushman, Denise E Sabatino

Development of AAV Variants with Human Hepatocyte Tropism and Neutralizing Antibody Escape Capacity

具有人类肝细胞趋向性和中和抗体逃逸能力的 AAV 变体的开发

Xiaolei Pei, Wenwei Shao, Allene Xing, Charles Askew, Xiaojing Chen, Caibin Cui, Yasmina L Abajas, David A Gerber, Elizabeth P Merricks, Timothy C Nichols, Wuping Li, R Jude Samulski, Chengwen Li

Influence of diabetes on the foreign body response to nitric oxide-releasing implants

糖尿病对异物对释放一氧化氮的植入物反应的影响

Robert J Soto, Elizabeth P Merricks, Dwight A Bellinger, Timothy C Nichols, Mark H Schoenfisch

An Observational Study from Long-Term AAV Re-administration in Two Hemophilia Dogs

对两只血友病犬进行长期 AAV 重复给药的观察性研究

Junjiang Sun, Wenwei Shao, Xiaojing Chen, Elizabeth P Merricks, Lauren Wimsey, Yasmina L Abajas, Glenn P Niemeyer, Clinton D Lothrop, Paul E Monahan, R Jude Samulski, Timothy C Nichols, Chengwen Li

Oxidized LDL and Fructosamine Associated with Severity of Coronary Artery Atherosclerosis in Insulin Resistant Pigs Fed a High Fat/High NaCl Diet

氧化低密度脂蛋白和果糖胺与饲喂高脂肪/高氯化钠饮食的胰岛素抵抗猪的冠状动脉粥样硬化严重程度相关

Timothy C Nichols, Elizabeth P Merricks, Dwight A Bellinger, Robin A Raymer, Jing Yu, Diana Lam, Gary G Koch, Walker H Busby Jr, David R Clemmons

Targeted disruption of LDLR causes hypercholesterolemia and atherosclerosis in Yucatan miniature pigs

LDLR 的靶向破坏导致尤卡坦小型猪出现高胆固醇血症和动脉粥样硬化

Bryan T Davis, Xiao-Jun Wang, Judy A Rohret, Jason T Struzynski, Elizabeth P Merricks, Dwight A Bellinger, Frank A Rohret, Timothy C Nichols, Christopher S Rogers