日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Cellular immunotherapy targeting CLL-1 for juvenile myelomonocytic leukemia

针对 CLL-1 的细胞免疫疗法治疗幼年型骨髓单核细胞白血病

Juwita Werner # ,Alex G Lee # ,Chujing Zhang ,Sydney Abelson ,Sherin Xirenayi ,Jose Rivera ,Khadija Yousuf ,Hanna Shin ,Bonell Patiño-Escobar ,Stefanie Bachl ,Kamal Mandal ,Abhilash Barpanda ,Emilio Ramos ,Adila Izgutdina ,Sibapriya Chaudhuri ,William C Temple ,Shubhmita Bhatnagar ,Jackson K Dardis ,Julia Meyer ,Carolina Morales ,Soheil Meshinchi ,Mignon L Loh ,Benjamin Braun ,Sarah K Tasian ,Arun P Wiita ,Elliot Stieglitz

Innate immune mechanisms hijacked by leukemia-initiating stem cells for selective advantage and immune evasion in Ptpn11-associated JMML

在Ptpn11相关的幼年型粒单核细胞白血病(JMML)中,白血病起始干细胞劫持先天免疫机制以获得选择性优势和免疫逃逸。

Hong Zheng ,Peng Zhao ,Zhenya Tan ,Wen-Mei Yu ,Juwita Werner ,Elliot Stieglitz ,Christopher C Porter ,Shanmuganathan Chandrakasan ,Daniel S Wechsler ,Simon Mendez-Ferrer ,Cheng-Kui Qu

Prototypical innate immune mechanism hijacked by leukemia-initiating mutant stem cells for selective advantage and immune evasion in Ptpn11-associated juvenile myelomonocytic leukemia

原型先天免疫机制被白血病起始突变干细胞劫持,在 Ptpn11 相关青少年粒单核细胞白血病中实现选择性优势和免疫逃避

Hong Zheng, Peng Zhao, Zhenya Tan, Wen-Mei Yu, Juwita Werner, Elliot Stieglitz, Chris Porter, Shanmuganathan Chandrakasan, Daniel Wechsler, Simon Mendez-Ferrer, Cheng-Kui Qu

Structural surfaceomics reveals an AML-specific conformation of integrin β2 as a CAR T cellular therapy target

结构表面组学揭示了整合素β2在急性髓系白血病(AML)中的特异性构象,并将其作为CAR-T细胞疗法的靶点。

Kamal Mandal,Gianina Wicaksono,Clinton Yu,Jarrett J Adams,Michael R Hoopmann,William C Temple,Adila Izgutdina,Bonell Patiño Escobar,Maryna Gorelik,Christian H Ihling,Matthew A Nix,Akul Naik,William H Xie,Juwita Hübner,Lisa A Rollins,Sandy M Reid,Emilio Ramos,Corynn Kasap,Veronica Steri,Juan Antonio Camara Serrano,Fernando Salangsang,Paul Phojanakong,Melanie McMillan,Victor Gavallos,Andrew D Leavitt,Aaron C Logan,Cliona M Rooney,Justin Eyquem,Andrea Sinz,Benjamin J Huang,Elliot Stieglitz,Catherine C Smith,Robert L Moritz,Sachdev S Sidhu,Lan Huang,Arun P Wiita

Allosteric SHP2 inhibition increases apoptotic dependency on BCL2 and synergizes with venetoclax in FLT3- and KIT-mutant AML

变构SHP2抑制增强了细胞凋亡对BCL2的依赖性,并与维奈托克在FLT3和KIT突变型急性髓系白血病中产生协同作用。

Bogdan Popescu,Carlos Stahlhut,Theodore C Tarver,Sydney Wishner,Bianca J Lee,Cheryl A C Peretz,Cuyler Luck,Paul Phojanakong,Juan Antonio Camara Serrano,Henry Hongo,Jose M Rivera,Simayijiang Xirenayi,John A Chukinas,Veronica Steri,Sarah K Tasian,Elliot Stieglitz,Catherine C Smith

Inhibition of BTK and PI3Kδ impairs the development of human JMML stem and progenitor cells

抑制BTK和PI3Kδ会损害人类幼年型粒单核细胞白血病(JMML)干细胞和祖细胞的发育。

Baskar Ramdas ,Lisa Deng Yuen ,Lakshmi Reddy Palam ,Roshini Patel ,Santhosh Kumar Pasupuleti ,Victoria Jideonwo ,Ji Zhang ,Callista Maguire ,Eric Wong ,Rahul Kanumuri ,Chujing Zhang ,George Sandusky ,Rebecca J Chan ,Chi Zhang ,Elliot Stieglitz ,Laura Haneline ,Reuben Kapur

Detection of a GLIS3 fusion in an infant with AML refractory to chemotherapy

在对化疗有耐药性的 AML 婴儿中检测出 GLIS3 融合

Stephen M Smith, Alex Lee, Schuyler Tong, Stanley Leung, Henry Hongo, Jose Rivera, Alejandro Sweet-Cordero, Jennifer Michlitsch, Elliot Stieglitz

Precision cancer monitoring using a novel, fully integrated, microfluidic array partitioning digital PCR platform

使用新型、完全集成的微流体阵列分区数字 PCR 平台进行精准癌症监测

Megan E Dueck, Robert Lin, Andrew Zayac, Steve Gallagher, Alexander K Chao, Lingxia Jiang, Sammy S Datwani, Paul Hung, Elliot Stieglitz

Predisposing germline mutations in high hyperdiploid acute lymphoblastic leukemia in children

儿童高超二倍体急性淋巴细胞白血病的易感种系突变

Adam J de Smith, Geneviève Lavoie, Kyle M Walsh, Sumeet Aujla, Erica Evans, Helen M Hansen, Ivan Smirnov, Alice Y Kang, Martin Zenker, John J Ceremsak, Elliot Stieglitz, Ivo S Muskens, William Roberts, Roberta McKean-Cowdin, Catherine Metayer, Philippe P Roux, Joseph L Wiemels

Genome-wide DNA methylation is predictive of outcome in juvenile myelomonocytic leukemia

全基因组 DNA 甲基化可预测青少年粒单核细胞白血病的结果

Elliot Stieglitz, Tali Mazor, Adam B Olshen, Huimin Geng, Laura C Gelston, Jon Akutagawa, Daniel B Lipka, Christoph Plass, Christian Flotho, Farid F Chehab, Benjamin S Braun, Joseph F Costello, Mignon L Loh5