日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Efficient elimination of MELAS-associated m.3243G mutant mitochondrial DNA by an engineered mitoARCUS nuclease

通过工程化的 mitoARCUS 核酸酶有效消除与 MELAS 相关的 m.3243G 突变线粒体 DNA

Wendy K Shoop, Janel Lape, Megan Trum, Alea Powell, Emma Sevigny, Adam Mischler, Sandra R Bacman, Flavia Fontanesi, Jeff Smith, Derek Jantz, Cassandra L Gorsuch, Carlos T Moraes

Targeting the hepatitis B cccDNA with a sequence-specific ARCUS nuclease to eliminate hepatitis B virus in vivo

利用序列特异性 ARCUS 核酸酶靶向乙肝 cccDNA 来消除体内乙肝病毒

Cassandra L Gorsuch, Paige Nemec, Mei Yu, Simin Xu, Dong Han, Jeff Smith, Janel Lape, Nicholas van Buuren, Ricardo Ramirez, Robert C Muench, Meghan M Holdorf, Becket Feierbach, Greg Falls, Jason Holt, Wendy Shoop, Emma Sevigny, Forrest Karriker, Robert V Brown, Amod Joshi, Tyler Goodwin, Ying K Tam,