JAK Inhibitor Therapy in a Child with Inherited USP18 Deficiency
JAK抑制剂治疗患有遗传性USP18缺乏症的儿童
期刊:New England Journal of Medicine
影响因子:78.5
doi:10.1056/NEJMoa1905633
Alsohime, Fahad; Martin-Fernandez, Marta; Temsah, Mohamad-Hani; Alabdulhafid, Majed; Le Voyer, Tom; Alghamdi, Malak; Qiu, Xueer; Alotaibi, Najla; Alkahtani, Areej; Buta, Sofija; Jouanguy, Emmanuelle; Al-Eyadhy, Ayman; Gruber, Conor; Hasan, Gamal M; Bashiri, Fahad A; Halwani, Rabih; Hassan, Hamdy H; Al-Muhsen, Saleh; Alkhamis, Nouf; Alsum, Zobaida; Casanova, Jean-Laurent; Bustamante, Jacinta; Bogunovic, Dusan; Alangari, Abdullah A