Correction of a urea cycle defect after ex vivo gene editing of human hepatocytes
人类肝细胞体外基因编辑后尿素循环缺陷的纠正
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2021.01.024
Mihaela Zabulica, Raghuraman C Srinivasan, Pinar Akcakaya, Gabriella Allegri, Burcu Bestas, Mike Firth, Christina Hammarstedt, Tomas Jakobsson, Towe Jakobsson, Ewa Ellis, Carl Jorns, Georgios Makris, Tanja Scherer, Nicole Rimann, Natalie R van Zuydam, Roberto Gramignoli, Anna Forslöw, Susanna Engber