日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A two-site collaborative study of electrical impedance myography for evaluation of disease progression in murine Duchenne muscular dystrophy models

一项双中心合作研究,利用电阻抗肌电图评估小鼠杜氏肌营养不良症模型中的疾病进展

Mantuano, Paola; van Putten, Maaike; Cobb, Buket Sonbas; Putker, Kayleigh; Boccanegra, Brigida; Tanganyika-de Winter, Christa; Tulimiero, Lisamaura; Schneider, Anne-Fleur; Cappellari, Ornella; Van De Vijver, Davy; Engelbeen, Sarah; Pandeya, Sarbesh; Nagy, Janice A; Rutkove, Seward

Learning, memory and blood-brain barrier pathology in Duchenne muscular dystrophy mice lacking Dp427, or Dp427 and Dp140

缺乏 Dp427 或 Dp427 和 Dp140 的杜氏肌营养不良症小鼠的学习、记忆和血脑屏障病理

Minou Verhaeg, Kevin Adamzek, Davy van de Vijver, Kayleigh Putker, Sarah Engelbeen, Daphne Wijnbergen, Maurice Overzier, Ernst Suidgeest, Louise van der Weerd, Annemieke Aartsma-Rus, Maaike van Putten

Efficient Downregulation of Alk4 in Skeletal Muscle After Systemic Treatment with Conjugated siRNAs in a Mouse Model for Duchenne Muscular Dystrophy

在杜氏肌营养不良症小鼠模型中,全身性应用偶联siRNA治疗后,骨骼肌中Alk4表达显著下调

Engelbeen, Sarah; Pasteuning-Vuhman, Svetlana; Boertje-van der Meulen, Joke; Parmar, Rubina; Charisse, Klaus; Sepp-Lorenzino, Laura; Manoharan, Muthiah; Aartsma-Rus, Annemieke; van Putten, Maaike

Challenges of Assessing Exon 53 Skipping of the Human DMD Transcript with Locked Nucleic Acid-Modified Antisense Oligonucleotides in a Mouse Model for Duchenne Muscular Dystrophy

在杜氏肌营养不良症小鼠模型中,使用锁定核酸修饰反义寡核苷酸评估人类 DMD 转录本外显子 53 跳跃的挑战

Sarah Engelbeen, Daniel O'Reilly, Davy Van De Vijver, Ingrid Verhaart, Maaike van Putten, Vignesh Hariharan, Matthew Hassler, Anastasia Khvorova, Masad J Damha, Annemieke Aartsma-Rus

Assessment of Behavioral Characteristics With Procedures of Minimal Human Interference in the mdx Mouse Model for Duchenne Muscular Dystrophy

利用人为干预最小的程序评估杜氏肌营养不良症mdx小鼠模型的行为特征

Engelbeen, Sarah; Aartsma-Rus, Annemieke; Koopmans, Bastijn; Loos, Maarten; van Putten, Maaike