First-in-human clinical study of an embryonic stem cell product for urea cycle disorders
首个针对尿素循环障碍的胚胎干细胞产品人体临床研究
期刊:Stem Cell Research & Therapy
影响因子:7.3
doi:10.1186/s13287-025-04162-3
Umezawa, Akihiro; Fukuda, Akinari; Horikawa, Reiko; Uchida, Hajime; Enosawa, Shin; Oishi, Yoshie; Nakamura, Naoko; Sasaki, Kengo; Yanagi, Yusuke; Shimizu, Seiichi; Nakao, Toshimasa; Kodama, Tasuku; Sakamoto, Seisuke; Hayakawa, Itaru; Akiyama, Saeko; Saku, Noriaki; Miyata, Shoko; Ite, Kenta; Javaregowda, Palaksha Kanive; Toyoda, Masashi; Nonaka, Hidenori; Nakamura, Kazuaki; Ito, Yoshikazu; Fukuhara, Yasuyuki; Miyazaki, Osamu; Nosaka, Shunsuke; Nakabayashi, Kazuhiko; Haga, Chizuko; Yoshioka, Takako; Masuda, Akira; Ohkura, Takashi; Yamazaki-Inoue, Mayu; Machida, Masakazu; Abutani-Sakamoto, Rie; Miyajima, Shoko; Akutsu, Hidenori; Matsubara, Yoichi; Igarashi, Takashi; Kasahara, Mureo