Targeting defective sphingosine kinase 1 in Niemann-Pick type C disease with an activator mitigates cholesterol accumulation
利用激活剂靶向尼曼匹克 C 型疾病中缺陷的鞘氨醇激酶 1 可减轻胆固醇的积累
期刊:Journal of Biological Chemistry
影响因子:4
doi:10.1074/jbc.RA120.012659
Jason Newton, Elisa N D Palladino, Cynthia Weigel, Michael Maceyka, Markus H Gräler, Can E Senkal, Ricardo D Enriz, Pavlina Marvanova, Josef Jampilek, Santiago Lima, Sheldon Milstien, Sarah Spiegel