日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Intrinsic muscle stem cell dysfunction underlies functional deficits in models of type 1 diabetes

内在肌肉干细胞功能障碍是1型糖尿病模型中功能缺陷的根本原因。

Chung, Jin D; Trieu, Jennifer; Parker, Benjamin L; Nguyen, John H; Chee, Annabel; Chan, Audrey S; Jayasimhan, Abhirup; Deliyanti, Devy; Houweling, Peter J; Voges, Holly K; Sourris, Karly C; Mills, Richard J; Coughlan, Melinda T; Wilkinson-Berka, Jennifer L; Porrello, Enzo R; Lynch, Gordon S

An FDA-approved drug structurally and phenotypically corrects the K210del mutation in genetic cardiomyopathy models.

FDA 批准的一种药物在结构和表型上纠正了遗传性心肌病模型中的 K210del 突变

Wang Ping, Ahmed Mahmoud Salama, Nguyen Ngoc Uyen Nhi, Menendez-Montes Ivan, Hsu Ching-Cheng, Farag Ayman B, Thet Suwannee, Lam Nicholas T, Wansapura Janaka P, Crossley Eric, Ma Ning, Zhao Shane Rui, Zhang Tiejun, Morimoto Sachio, Singh Rohit, Elhelaly Waleed, Tassin Tara C, Cardoso Alisson C, Williams Noelle S, Pointer Hayley L, Elliott David A, McNamara James W, Watt Kevin I, Porrello Enzo R, Sadayappan Sakthivel, Sadek Hesham A

Automated integration of multi-slice spatial transcriptomics data in 2D and 3D using VR-Omics

利用VR-Omics实现二维和三维多层空间转录组学数据的自动整合

Bienroth, Denis; Charitakis, Natalie; Wong, Dillon; Zhang, Yunhan C; Jaeger-Honz, Sabrina; Ding, Jialin; Watt, Kevin I; Stolper, Julian; Chambers-Smith, Hazel; MacGregor, Duncan; Christiansen, Bronwyn; Vivien, Celine; Piers, Adam T; Waylen, Lisa N; Hoffmann, Lucas B; Tang, Jessica; La, Hue M; Du, Mei R M; Mohenska, Monika; Polo, Jose M; Grimmond, Sean; Scott, Ethan; Rossello, Fernando J; Porrello, Enzo R; Klein, Karsten; Nim, Hieu T; Elliott, David A; Schreiber, Falk; Ramialison, Mirana

Maturation of human cardiac organoids enables complex disease modeling and drug discovery

人类心脏类器官的成熟使得复杂疾病建模和药物发现成为可能。

Pocock, Mark W; Reid, Janice D; Robinson, Harley R; Charitakis, Natalie; Krycer, James R; Foster, Simon R; Fitzsimmons, Rebecca L; Lor, Mary; Devilée, Lynn A C; Batho, Christopher A P; Tuano, Natasha; Howden, Sara E; Vlahos, Katerina; Watt, Kevin I; Piers, Adam T; Bibby, Kaitlyn; McNamara, James W; Sutton, Rebecca; Iaprintsev, Valerii; Mathew, Jacob; Voges, Holly K; Fortuna, Patrick R J; Bass-Stringer, Sebastian; Vivien, Celine; Rae, James; Parton, Robert G; Firulli, Anthony B; Lisowski, Leszek; Huckstep, Hannah; Humphrey, Sean J; Lal, Sean; Konstantinov, Igor E; Weintraub, Robert G; Elliott, David A; Ramialison, Mirana; Porrello, Enzo R; Mills, Richard J; Hudson, James E

Kidney organoids reveal redundancy in viral entry pathways during ACE2-dependent SARS-CoV-2 infection

肾脏类器官揭示了ACE2依赖性SARS-CoV-2感染过程中病毒进入途径的冗余性

Jessica M Vanslambrouck # ,Jessica A Neil # ,Rajeev Rudraraju # ,Sophia Mah ,Ker Sin Tan ,Ella Groenewegen ,Thomas A Forbes ,Katerina Karavendzas ,David A Elliott ,Enzo R Porrello ,Kanta Subbarao # ,Melissa H Little #

Disparities in spatially variable gene calling highlight the need for benchmarking spatial transcriptomics methods

空间变异基因调用结果的差异凸显了对空间转录组学方法进行基准测试的必要性。

Charitakis, Natalie; Salim, Agus; Piers, Adam T; Watt, Kevin I; Porrello, Enzo R; Elliott, David A; Ramialison, Mirana

Alpha kinase 3 signaling at the M-band maintains sarcomere integrity and proteostasis in striated muscle

α激酶3在M带处的信号传导维持横纹肌的肌节完整性和蛋白质稳态。

James W McNamara ,Benjamin L Parker ,Holly K Voges ,Neda R Mehdiabadi ,Francesca Bolk ,Feroz Ahmad ,Jin D Chung ,Natalie Charitakis ,Jeffrey Molendijk ,Antonia T L Zech ,Sean Lal ,Mirana Ramialison ,Kathy Karavendzas ,Hayley L Pointer ,Petros Syrris ,Luis R Lopes ,Perry M Elliott ,Gordon S Lynch ,Richard J Mills ,James E Hudson ,Kevin I Watt ,Enzo R Porrello # ,David A Elliott #

GLA-modified RNA treatment lowers GB3 levels in iPSC-derived cardiomyocytes from Fabry-affected individuals

GLA修饰的RNA治疗可降低法布里病患者iPSC来源心肌细胞中的GB3水平

Ter Huurne, Menno; Parker, Benjamin L; Liu, Ning Qing; Qian, Elizabeth Ling; Vivien, Celine; Karavendzas, Kathy; Mills, Richard J; Saville, Jennifer T; Abu-Bonsrah, Dad; Wise, Andrea F; Hudson, James E; Talbot, Andrew S; Finn, Patrick F; Martini, Paolo G V; Fuller, Maria; Ricardo, Sharon D; Watt, Kevin I; Nicholls, Kathy M; Porrello, Enzo R; Elliott, David A

Sox7-positive endothelial progenitors establish coronary arteries and govern ventricular compaction

Sox7阳性内皮祖细胞形成冠状动脉并控制心室致密化

Ivy Kn Chiang ,David Humphrey ,Richard J Mills ,Peter Kaltzis ,Shikha Pachauri ,Matthew Graus ,Diptarka Saha ,Zhijian Wu ,Paul Young ,Choon Boon Sim ,Tara Davidson ,Andres Hernandez-Garcia ,Chad A Shaw ,Alexander Renwick ,Daryl A Scott ,Enzo R Porrello ,Emily S Wong ,James E Hudson ,Kristy Red-Horse ,Gonzalo Del Monte-Nieto ,Mathias Francois

Generation of vascularized human cardiac organoids for 3D in vitro modeling

生成血管化人类心脏类器官用于 3D 体外建模

Holly K Voges, Richard J Mills, Enzo R Porrello, James E Hudson