日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

CRISPR/Cas9 generated knockout mice lacking phenylalanine hydroxylase protein as a novel preclinical model for human phenylketonuria

CRISPR/Cas9 生成缺乏苯丙氨酸羟化酶蛋白的敲除小鼠,作为人类苯丙酮尿症的新型临床前模型

Kuldeep Singh, Cathleen S Cornell, Robert Jackson, Mostafa Kabiri, Michael Phipps, Mitul Desai, Robert Fogle, Xiaoyou Ying, Gulbenk Anarat-Cappillino, Sarah Geller, Jennifer Johnson, Errin Roberts, Katie Malley, Tim Devlin, Matthew DeRiso, Patricia Berthelette, Yao V Zhang, Susan Ryan, Srinivas Rao,

Inhibition of TGF-β Increases Bone Volume and Strength in a Mouse Model of Osteogenesis Imperfecta

抑制 TGF-β 可增加成骨不全症小鼠模型中的骨体积和强度

Benjamin Greene, Ryan J Russo, Shannon Dwyer, Katie Malley, Errin Roberts, Joseph Serrielo, Peter Piepenhagen, Sheila Cummings, Susan Ryan, Christine Zarazinski, Sasidhar Uppuganti, Nikolai Bukanov, Jeffry S Nyman, Megan K Cox, Shiguang Liu, Oxana Ibraghimov-Beskrovnaya, Yves Sabbagh

An experimental model of anti-PD-1 resistance exhibits activation of TGFß and Notch pathways and is sensitive to local mRNA immunotherapy

抗 PD-1 耐药的实验模型表现出 TGFβ 和 Notch 通路的激活,并且对局部 mRNA 免疫疗法敏感

Marie Bernardo, Tatiana Tolstykh, Yu-An Zhang, Dinesh S Bangari, Hui Cao, Kerstin A Heyl, Joon Sang Lee, Natalia V Malkova, Katie Malley, Eladio Marquez, Jack Pollard, Hui Qu, Errin Roberts, Sue Ryan, Kuldeep Singh, Fangxian Sun, Emma Wang, Keith Bahjat, Dmitri Wiederschain, Timothy R Wagenaar

Gene delivery of a modified antibody to Aβ reduces progression of murine Alzheimer's disease

将修饰抗体基因导入小鼠体内可减缓小鼠阿尔茨海默病的发展进程。

Bradford M Elmer ,Kurt A Swanson ,Dinesh S Bangari ,Peter A Piepenhagen ,Errin Roberts ,Tatyana Taksir ,Lei Guo ,Maria-Carmen Obinu ,Pascal Barneoud ,Susan Ryan ,Bailin Zhang ,Laurent Pradier ,Zhi-Yong Yang ,Gary J Nabel