VCP/p97 inhibitor CB-5083 modulates muscle pathology in a mouse model of VCP inclusion body myopathy
VCP/p97 抑制剂 CB-5083 调节 VCP 包涵体肌病小鼠模型中的肌肉病理
期刊:Journal of Translational Medicine
影响因子:6.1
doi:10.1186/s12967-021-03186-6
Cheng Cheng, Lan Weiss, Henri Leinonen, Alyaa Shmara, Hong Z Yin, Timothy Ton, Annie Do, Jonathan Lee, Lac Ta, Eshanee Mohanty, Jesse Vargas, John Weiss, Krzysztof Palczewski, Virginia Kimonis0