日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Clonal selection of hematopoietic stem cells after gene therapy for sickle cell disease

镰状细胞病基因治疗后造血干细胞的克隆选择

Michael Spencer Chapman #, Alyssa H Cull #, Marioara F Ciuculescu, Erica B Esrick, Emily Mitchell, Hyunchul Jung, Laura O'Neill, Kirsty Roberts, Margarete A Fabre, Nicholas Williams, Jyoti Nangalia, Joanne Quinton, James M Fox, Danilo Pellin, Julie Makani, Myriam Armant, David A Williams, Peter J Ca

Secondary Neoplasms After Hematopoietic Cell Transplant for Sickle Cell Disease

镰状细胞病造血干细胞移植后的继发性肿瘤

Eapen, Mary; Brazauskas, Ruta; Williams, David A; Walters, Mark C; St Martin, Andrew; Jacobs, Benjamin L; Antin, Joseph H; Bona, Kira; Chaudhury, Sonali; Coleman-Cowger, Victoria H; DiFronzo, Nancy L; Esrick, Erica B; Field, Joshua J; Fitzhugh, Courtney D; Kanter, Julie; Kapoor, Neena; Kohn, Donald B; Krishnamurti, Lakshmanan; London, Wendy B; Pulsipher, Michael A; Talib, Sohel; Thompson, Alexis A; Waller, Edmund K; Wun, Ted; Horowitz, Mary M

Defining global strategies to improve outcomes in sickle cell disease: a Lancet Haematology Commission

制定改善镰状细胞病治疗效果的全球战略:柳叶刀血液学委员会

Piel, Frédéric B; Rees, David C; DeBaun, Michael R; Nnodu, Obiageli; Ranque, Brigitte; Thompson, Alexis A; Ware, Russell E; Abboud, Miguel R; Abraham, Allistair; Ambrose, Emmanuela E; Andemariam, Biree; Colah, Roshan; Colombatti, Raffaella; Conran, Nicola; Costa, Fernando F; Cronin, Robert M; de Montalembert, Mariane; Elion, Jacques; Esrick, Erica; Greenway, Anthea L; Idris, Ibrahim M; Issom, David-Zacharie; Jain, Dipty; Jordan, Lori C; Kaplan, Zane S; King, Allison A; Lloyd-Puryear, Michele; Oppong, Samuel A; Sharma, Akshay; Sung, Lillian; Tshilolo, Leon; Wilkie, Diana J; Ohene-Frempong, Kwaku

Genetic reversal of the globin switch concurrently modulates both fetal and sickle hemoglobin and reduces red cell sickling

珠蛋白转换的基因逆转可同时调节胎儿血红蛋白和镰状血红蛋白,并减少红细胞镰状化。

Daniel C De Souza # ,Nicolas Hebert # ,Erica B Esrick ,M Felicia Ciuculescu ,Natasha M Archer ,Myriam Armant ,Étienne Audureau ,Christian Brendel ,Giuseppe Di Caprio ,Frédéric Galactéros ,Donghui Liu ,Amanda McCabe ,Emily Morris ,Ethan Schonbrun ,Dillon Williams ,David K Wood ,David A Williams ,Pablo Bartolucci ,John M Higgins

Bidirectional processes linking social determinants of health and pediatric sickle cell anemia management: A qualitative study

社会健康决定因素与儿童镰状细胞贫血症管理之间的双向过程:一项定性研究

Long, Kristin A; Blakey, Ariel O; Amaro, Christina M; Eilenberg, Jenna S; Brochier, Annelise; Garg, Arvin; Drainoni, Mari-Lynn; Pashankar, Farzana; Esrick, Erica B; Kavanagh, Patricia L

Metformin for treatment of cytopenias in children and young adults with Fanconi anemia

二甲双胍用于治疗范可尼贫血症患儿和青少年的血细胞减少症

Pollard, Jessica A; Furutani, Elissa; Liu, Shanshan; Esrick, Erica; Cohen, Laurie E; Bledsoe, Jacob; Liu, Chih-Wei; Lu, Kun; de Haro, Maria Jose Ramirez; Surrallés, Jordi; Malsch, Maggie; Kuniholm, Ashley; Galvin, Ashley; Armant, Myriam; Kim, Annette S; Ballotti, Kaitlyn; Moreau, Lisa; Zhou, Yu; Babushok, Daria; Boulad, Farid; Carroll, Clint; Hartung, Helge; Hont, Amy; Nakano, Taizo; Olson, Tim; Sze, Sei-Gyung; Thompson, Alexis A; Wlodarski, Marcin W; Gu, Xuesong; Libermann, Towia A; D'Andrea, Alan; Grompe, Markus; Weller, Edie; Shimamura, Akiko

A Rare Presentation of Rickets Mimicking Sacroiliitis: A Case Report and Literature Review

佝偻病罕见表现为骶髂关节炎:病例报告及文献综述

Ali, Rafal S; Abdulhussein, Roua; Esrick, Michael; Sen, Mitali

Post-Transcriptional Genetic Silencing of BCL11A to Treat Sickle Cell Disease

利用转录后基因沉默技术沉默BCL11A基因治疗镰状细胞病

Esrick, Erica B; Lehmann, Leslie E; Biffi, Alessandra; Achebe, Maureen; Brendel, Christian; Ciuculescu, Marioara F; Daley, Heather; MacKinnon, Brenda; Morris, Emily; Federico, Amy; Abriss, Daniela; Boardman, Kari; Khelladi, Radia; Shaw, Kit; Negre, Helene; Negre, Olivier; Nikiforow, Sarah; Ritz, Jerome; Pai, Sung-Yun; London, Wendy B; Dansereau, Colleen; Heeney, Matthew M; Armant, Myriam; Manis, John P; Williams, David A

β-Thalassemia: evolving treatment options beyond transfusion and iron chelation

β-地中海贫血:除输血和铁螯合外,治疗选择正在不断发展

Langer, Arielle L; Esrick, Erica B

Preclinical Evaluation of a Novel Lentiviral Vector Driving Lineage-Specific BCL11A Knockdown for Sickle Cell Gene Therapy

新型慢病毒载体驱动谱系特异性 BCL11A 敲低用于镰状细胞基因治疗的临床前评估

Christian Brendel, Olivier Negre, Michael Rothe, Swaroopa Guda, Geoff Parsons, Chad Harris, Meaghan McGuinness, Daniela Abriss, Alla Tsytsykova, Denise Klatt, Martin Bentler, Danilo Pellin, Lauryn Christiansen, Axel Schambach, John Manis, Helene Trebeden-Negre, Melissa Bonner, Erica Esrick, Gabor Ve