Splice modulation of COL4A5 reinstates collagen IV assembly in an organoid model of Alport syndrome
在Alport综合征类器官模型中，COL4A5的剪接调控可恢复IV型胶原的组装。
期刊:JCI Insight
影响因子:6.1
doi:10.1172/jci.insight.194759
Saei, Hassan; Estebe, Bruno; Goudin, Nicolas; Esmailpour, Mahsa; Haure, Julie; Gribouval, Olivier; Arrondel, Christelle; Moriniere, Vincent; Tian, Pinyuan; Lennon, Rachel; Antignac, Corinne; Mollet, Geraldine; Dorval, Guillaume
