日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Gene editing without ex vivo culture evades genotoxicity in human hematopoietic stem cells

无需体外培养的基因编辑可避免对人类造血干细胞造成基因毒性。

Jing Zeng ,My Anh Nguyen ,Pengpeng Liu ,Lucas Ferreira da Silva ,Sébastien Levesque ,Linda Y Lin ,David G Justus ,Karl Petri ,Kendell Clement ,Shaina N Porter ,Archana Verma ,Nola R Neri ,Tolulope Rosanwo ,Marioara-Felicia Ciuculescu ,Daniela Abriss ,Esther Mintzer ,Stacy A Maitland ,Selami Demirci ,Hye Ji Cha ,Stuart H Orkin ,John F Tisdale ,David A Williams ,Lihua Julie Zhu ,Shondra M Pruett-Miller ,Luca Pinello ,J Keith Joung ,Vikram Pattanayak ,John P Manis ,Myriam Armant ,Danilo Pellin ,Christian Brendel ,Scot A Wolfe ,Daniel E Bauer

Transcriptional and chromatin profiling of human blood innate lymphoid cell subsets sheds light on HIV-1 pathogenesis

人类血液固有淋巴细胞亚群的转录和染色质谱分析揭示了HIV-1的发病机制

Yetao Wang ,Lawrence Lifshitz ,Noah J Silverstein ,Esther Mintzer ,Kevin Luk ,Pamela StLouis ,Michael A Brehm ,Scot A Wolfe ,Steven G Deeks ,Jeremy Luban

Comparative Transcriptome Analysis of Acne vulgaris, Rosacea, and Hidradenitis Suppurativa Supports High Dose Dietary Zinc as a Therapeutic Agent

寻常痤疮、酒渣鼻和化脓性汗腺炎的比较转录组分析支持高剂量膳食锌作为治疗剂

Li Li, Irshad Hajam, Jean S McGee, Zhengkuan Tang, Ye Zhang, Nikil Badey, Esther Mintzer, Zhenrui Zhang, George Y Liu, George M Church, Yu Wang

Genome-wide detection of CRISPR editing in vivo using GUIDE-tag

使用 GUIDE 标签进行体内全基因组 CRISPR 编辑检测

Shun-Qing Liang #, Pengpeng Liu #, Jordan L Smith, Esther Mintzer, Stacy Maitland, Xiaolong Dong, Qiyuan Yang, Jonathan Lee, Cole M Haynes, Lihua Julie Zhu, Jonathan K Watts, Erik J Sontheimer, Scot A Wolfe, Wen Xue

Efficient Homology-Directed Repair with Circular Single-Stranded DNA Donors

利用环状单链DNA供体进行高效的同源定向修复

Sukanya Iyer,Aamir Mir,Joel Vega-Badillo,Benjamin P Roscoe,Raed Ibraheim,Lihua Julie Zhu,Jooyoung Lee,Pengpeng Liu,Kevin Luk,Esther Mintzer,Dongsheng Guo,Josias Soares de Brito,Charles P Emerson Jr,Phillip D Zamore,Erik J Sontheimer,Scot A Wolfe

Improved prime editors enable pathogenic allele correction and cancer modelling in adult mice

改进的 prime editor 能够在成年小鼠中进行致病等位基因校正和癌症建模

Pengpeng Liu #, Shun-Qing Liang #, Chunwei Zheng, Esther Mintzer, Yan G Zhao, Karthikeyan Ponnienselvan, Aamir Mir, Erik J Sontheimer, Guangping Gao, Terence R Flotte, Scot A Wolfe, Wen Xue

Self-inactivating, all-in-one AAV vectors for precision Cas9 genome editing via homology-directed repair in vivo

用于通过体内同源定向修复进行精准Cas9基因组编辑的自失活一体化AAV载体

Raed Ibraheim ,Phillip W L Tai ,Aamir Mir ,Nida Javeed ,Jiaming Wang ,Tomás C Rodríguez ,Suk Namkung ,Samantha Nelson ,Eraj Shafiq Khokhar ,Esther Mintzer ,Stacy Maitland ,Zexiang Chen ,Yueying Cao ,Emmanouela Tsagkaraki ,Scot A Wolfe ,Dan Wang ,Athma A Pai ,Wen Xue ,Guangping Gao ,Erik J Sontheimer

Enhanced Cas12a editing in mammalian cells and zebrafish

哺乳动物细胞和斑马鱼中增强的 Cas12a 编辑

Pengpeng Liu, Kevin Luk, Masahiro Shin, Feston Idrizi, Samantha Kwok, Benjamin Roscoe, Esther Mintzer, Sneha Suresh, Kyle Morrison, Josias B Frazão, Mehmet Fatih Bolukbasi, Karthikeyan Ponnienselvan, Jeremy Luban, Lihua Julie Zhu, Nathan D Lawson, Scot A Wolfe