Self-inactivating, all-in-one AAV vectors for precision Cas9 genome editing via homology-directed repair in vivo
用于通过体内同源定向修复进行精准Cas9基因组编辑的自失活一体化AAV载体
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-021-26518-y
Raed Ibraheim ,Phillip W L Tai ,Aamir Mir ,Nida Javeed ,Jiaming Wang ,Tomás C Rodríguez ,Suk Namkung ,Samantha Nelson ,Eraj Shafiq Khokhar ,Esther Mintzer ,Stacy Maitland ,Zexiang Chen ,Yueying Cao ,Emmanouela Tsagkaraki ,Scot A Wolfe ,Dan Wang ,Athma A Pai ,Wen Xue ,Guangping Gao ,Erik J Sontheimer