日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

The TransEuro open-label trial of human fetal ventral mesencephalic transplantation in patients with moderate Parkinson's disease

TransEuro 是一项开放标签试验,旨在研究人类胎儿腹侧中脑移植治疗中度帕金森病患者的疗效。

Barker, Roger A; Lao-Kaim, Nicholas P; Guzman, Natalie Valle; Athauda, Dilan; Bjartmarz, Hjalmar; Björklund, Anders; Church, Alistair; Cutting, Emma; Daft, Danielle; Dayal, Viswas; Dunnett, Stephen; Evans, Amy; Grealish, Shane; Hannaway, Naomi; He, Xiaoling; Hewitt, Sam; Kefalopoulou, Zinovia; Mahlknecht, Philipp; Martín-Bastida, Antonio; Farrell, Krista; Moore, Sarah; Bulstrode, Harry; Nakornchai, Tagore; Nelander-Wahlestedt, Jenny; Roupé, Linnea; Paul, Gesine; Peall, Kathryn; Rosser, Anne; Roca-Fernández, Adriana; Rowlands, Sophie; McGorrian, Anne-Marie; Scherf, Caroline; Vinh, Ngoc Nga; Roberton, Victoria; Kelly, Claire; Lelos, Mariah; Torres, Eduardo; Shires, Kate; Hills, Rachel; Williams, Debbie; Roussakis, Andreas-Antonios; Sibley, Krista; Tyers, Pamela; Wijeyekoon, Ruwani; Williams-Gray, Caroline; Foltynie, Thomas; Piccini, Paola; Morris, Robert; Lazic, Stanley E; Lindvall, Olle; Parmar, Malin; Widner, Hakan

Genotype-first approach reveals monogenic lipodystrophy is underdiagnosed, with health and mortality risks

基因型优先检测方法揭示单基因脂肪营养不良症诊断不足,存在健康和死亡风险。

Sharp, Luke N; Colclough, Kevin; Murray Leech, Jacques; Evans, Amy V; Hattersley, Andrew T; Weedon, Michael N; Brown, Rebecca J; Patel, Kashyap A

Reassessing the role of the p.(Arg304Gln) missense AIP variant in pituitary tumorigenesis

重新评估 p.(Arg304Gln) 错义 AIP 变异在垂体肿瘤发生中的作用

Loughrey, Paul Benjamin; Mothojakan, Nadira B; Iacovazzo, Donato; Arni, Ankit; Aflorei, Elena D; Arnaldi, Giorgio; Barlier, Anne; Beckers, Albert; Bizzi, Mariana F; Chanson, Philippe; Dal, Jakob; Daly, Adrian F; Dang, Mary N; David, Alessia; Andrade, Matheus de Oliveira; Else, Tobias; Elston, Marianne S; Evans, Amy; Ferrau, Francesco; Fica, Simona; Flanagan, Daniel; Gadelha, Monica R; Grossman, Ashley B; Kapur, Sonal; Khoo, Bernard; Kumar, Ajith V; Kumar-Sinha, Chandan; Lechan, Ronald M; Ludman, Mark; Metherell, Louise A; Miljic, Dragana; Mourougavelou, Vishnou; Musat, Madalina; Occhi, Gianluca; Owens, Martina; Pascanu, Ionela; Pinheiro, Sergio V B; Radian, Serban; Ribeiro-Oliveira, Antonio; Schöfl, Christof; Patel, Kashyap A; Hernández-Ramírez, Laura C; Korbonits, Márta

Endocrine Alterations in Patients With Pachydermoperiostosis

厚皮骨膜炎患者的内分泌改变

Stelmachowska-Banaś, Maria; Barry, Sayka; Angurala, Ishita; Rice, Tom; Magid, Kesson; Carreira, Ana; Rai, Ashutosh; Evans, Amy; Bollington, Mark; Kaur, Vaishali; Singhmar, Shallu; Silaghi, Cristina Alina; Mandisodza, Kudakwashe; McGregor, Alan; Sahoo, Jayaprakash; Gupta, Rahul; Behera, Kishore Kumar; Roy, Ayan; Carr, Ian M; Loughrey, Paul Benjamin; Dutta, Pinaki; Korbonits, Márta

Delivery of a Muscle-Targeted Adeno-Associated Vector Via Ex Vivo Normothermic Perfusion Is Efficient, Durable, and Safe in a Preclinical Porcine Heart Transplant Model

在临床前猪心脏移植模型中,通过体外常温灌注递送肌肉靶向腺相关载体是高效、持久且安全的。

Dewan, Krish C; Chen, Jeng-Wei; Lobo, Alejandro A; Gross, Ryan T; Wang, Chunbo; Rivera, Karla G; Tran, Keely Dieplin; Ngeve, Smith; Johnston, Violet G; Wendell, David; Glass, Carolyn K; Evans, Amy; Ho, Sam; Lezberg, Paul; Casy, Widler; Bazile, Marla; Patel, Kruti; Cockrell, Adam S; Milano, Carmelo A; Bowles, Dawn

A porcine model of acute rejection for cardiac transplantation.

猪心脏移植急性排斥反应模型

Mendiola Pla Michelle, Chiang Yuting, Glass Carolyn, Wendell David C, Swain-Lenz Devjanee, Ho Sam, Fudim Marat, Lee Franklin H, Kang Lillian, Smith Matthew F, Alvarez Lobo Alejandro, Mitra Kishen, Gross Ryan T, Wang Chunbo, Bishawi Muath, Vekstein Andrew, Dewan Krish, Chen JengWei, Evans Amy, Roki Antonio, Ferrell Paul, Oristian Kristianne M, Pizzo Salvatore V, Li Jie, Hale Laura P, Lezberg Paul M, Milano Carmelo A, Bowles Dawn E

STEM-PD trial protocol: a multi-centre, single-arm, first-in-human, dose-escalation trial, investigating the safety and tolerability of intraputamenal transplantation of human embryonic stem cell-derived dopaminergic cells for Parkinson's disease

STEM-PD试验方案:一项多中心、单组、首次人体剂量递增试验,旨在研究壳核内移植人胚胎干细胞衍生多巴胺能细胞治疗帕金森病的安全性和耐受性。

Paul, Gesine; Bjartmarz, Hjalmar; Björklund, Anders; Cutting, Emma; Evans, Amy; Harry, Bronwen; Hansson, Oskar; Kayhanian, Saeed; Kirkeby, Agnete; Lao-Kim, Nicholas; Lindvall, Olle; Nelander, Jenny; Piccini, Paola; Smith, Ruben; Ullén, Susann; Van Vliet, Trinette; Widner, Hakan; Parmar, Malin; Barker, Roger A

A High-Fidelity Porcine Model of Orthotopic Heart Transplantation Following Donation after Circulatory Death

循环死亡后捐献的猪原位心脏移植高保真模型

Dewan, Krish C; Benkert, Abigail R; Lobo, Alejandro A; Chen, Jengwei; Gross, Ryan T; Salinas, Martha; Evans, Amy; Achanta, Satyanarayana; Mehta, Sachin; Cutrone, Michael; Johnston, Violet; Rivera, Karla; Tran, Keely Dieplinh; Ngeve, Smith; McCartney, Sharon; Milano, Carmelo; Bowles, Dawn E; Keenan, Jeffrey E

E7-mediated repression of miR-203 promotes LASP1-dependent proliferation in HPV-positive cervical cancer

E7 介导的 miR-203 抑制促进 HPV 阳性宫颈癌中的 LASP1 依赖性增殖

Molly R Patterson, Aniek S Meijers, Emma L Ryder, Louisa M Wootton, James A Scarth, Debra Evans, Amy L Turner, Christopher W Wasson, Janne E Darell, Daisy A Theobald, Joseph A Cogan, Claire D James, Miao Wang, John E Ladbury, Iain M Morgan, Adel Samson, Ethan L Morgan, Andrew Macdonald

APOA2 increases cholesterol efflux capacity to plasma HDL by displacing the C-terminus of resident APOA1

APOA2 通过取代驻留 APOA1 的 C 端,增加胆固醇向血浆 HDL 的外排能力。

Snigdha Sarkar ,Jamie Morris ,Youngki You ,Hannah Sexmith ,Scott E Street ,Stephanie M Thibert ,Isaac K Attah ,Chelsea M Hutchinson Bunch ,Irina V Novikova ,James E Evans ,Amy S Shah ,Scott M Gordon ,Jere P Segrest ,Karin E Bornfeldt ,Tomas Vaisar ,Jay W Heinecke ,W Sean Davidson ,John T Melchior