FORCE platform overcomes barriers of oligonucleotide delivery to muscle and corrects myotonic dystrophy features in preclinical models
FORCE 平台克服了寡核苷酸输送到肌肉的障碍,并纠正了临床前模型中的强直性肌营养不良症特征
期刊:Commun Med (Lond)
影响因子:
doi:10.1038/s43856-025-00733-w
Timothy Weeden, Tyler Picariello, Brendan Quinn, Sean Spring, Pei-Yi Shen, Qifeng Qiu, Benjamin F Vieira, Lydia Schlaefke, Ryan J Russo, Ya-An Chang, Jin Cui, Monica Yao, Aiyun Wen, Nelson Hsia, Tama Evron, Katy Ovington, Pei-Ni Tsai, Nicholas Yoder, Bo Lan, Reshmii Venkatesan, John Hall, Cody A Des