CFTR gene transfer with AAV improves early cystic fibrosis pig phenotypes
CFTR 基因转移与 AAV 改善早期囊性纤维化猪表型
期刊:JCI Insight
影响因子:6.3
doi:10.1172/jci.insight.88728
Benjamin Steines, David D Dickey, Jamie Bergen, Katherine Jda Excoffon, John R Weinstein, Xiaopeng Li, Ziying Yan, Mahmoud H Abou Alaiwa, Viral S Shah, Drake C Bouzek, Linda S Powers, Nicholas D Gansemer, Lynda S Ostedgaard, John F Engelhardt, David A Stoltz, Michael J Welsh, Patrick L Sinn, David V