Translational enhancement by base editing of the Kozak sequence rescues haploinsufficiency
通过碱基编辑 Kozak 序列实现翻译增强,挽救单倍体不足
期刊:Nucleic Acids Research
影响因子:16.6
doi:10.1093/nar/gkac799
Chiara Ambrosini, Eliana Destefanis, Eyemen Kheir, Francesca Broso, Federica Alessandrini, Sara Longhi, Nicolò Battisti, Isabella Pesce, Erik Dassi, Gianluca Petris, Anna Cereseto, Alessandro Quattrone