A GLP-Compliant Toxicology and Biodistribution Study: Systemic Delivery of an rAAV9 Vector for the Treatment of Mucopolysaccharidosis IIIB
符合 GLP 标准的毒理学和生物分布研究:系统性递送 rAAV9 载体用于治疗粘多糖贮积症 IIIB
期刊:Human Gene Therapy Clinical Development
影响因子:
doi:10.1089/humc.2015.132
Aaron S Meadows, F Jason Duncan, Marybeth Camboni, Kathryn Waligura, Chrystal Montgomery, Kimberly Zaraspe, Bartholomew J Naughton, William G Bremer, Christopher Shilling, Christopher M Walker, Brad Bolon, Kevin M Flanigan, Kim L McBride, Douglas M McCarty, Haiyan Fu