Gene Therapy of Dominant CRX-Leber Congenital Amaurosis using Patient Stem Cell-Derived Retinal Organoids
利用患者干细胞衍生的视网膜类器官进行显性CRX-Leber先天性黑蒙的基因治疗
期刊:Stem Cell Reports
影响因子:5.1
doi:10.1016/j.stemcr.2020.12.018
Kruczek, Kamil; Qu, Zepeng; Gentry, James; Fadl, Benjamin R; Gieser, Linn; Hiriyanna, Suja; Batz, Zachary; Samant, Mugdha; Samanta, Ananya; Chu, Colin J; Campello, Laura; Brooks, Brian P; Wu, Zhijian; Swaroop, Anand
细胞生物学
基因治疗
干细胞
3D/类器官
发育与干细胞
CRX
