日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Efficacy and Safety of Aficamten in Children and Adolescents With Obstructive Hypertrophic Cardiomyopathy: Study Design and Rationale of CEDAR-HCM

Aficamten治疗儿童和青少年梗阻性肥厚型心肌病的疗效和安全性:CEDAR-HCM研究的设计和原理

Kaski, Juan Pablo; Kantor, Paul F; Nakano, Stephanie J; Olivotto, Iacopo; Russell, Mark W; Godown, Justin; Chiu, Michael; German, Polina; Heitner, Stephen B; Jacoby, Daniel L; Kupfer, Stuart; Lutz, Justin; Maharao, Neha; Malik, Fady I; Melloni, Chiara; Nieto Morales, Paula F; Simkins, Tyrell; Wei, Jenny; Ho, Carolyn Y

Efficacy of aficamten in patients with obstructive hypertrophic cardiomyopathy and mild symptoms: results from the SEQUOIA-HCM trial

阿菲卡坦治疗梗阻性肥厚型心肌病伴轻度症状患者的疗效:SEQUOIA-HCM试验结果

Maron, Martin S; Gimeno, Juan Ramon; Veselka, Josef; Barriales-Villa, Roberto; Claggett, Brian L; Coats, Caroline J; Hegde, Sheila M; Januzzi, James L; Kulac, Ian J; Masri, Ahmad; Nassif, Michael E; Spertus, John A; Jacoby, Daniel L; Heitner, Stephen B; Kupfer, Stuart; Malik, Fady I; Wohltman, Amy; Olivotto, Iacopo

Reldesemtiv in Amyotrophic Lateral Sclerosis: Results From the COURAGE-ALS Randomized Clinical Trial

Reldesemtiv治疗肌萎缩侧索硬化症:COURAGE-ALS随机临床试验结果

Shefner, Jeremy M; Cudkowicz, Merit E; Genge, Angela; Hardiman, Orla; Al-Chalabi, Ammar; Andrews, Jinsy A; Chio, Adriano; Corcia, Philippe; Couratier, Philippe; de Carvalho, Mamede; Heiman-Patterson, Terry; Henderson, Robert D; Ingre, Caroline; Johnston, Wendy; Ludolph, Albert; Maragakis, Nicholas J; Miller, Timothy M; Mora, Jesus S; Petri, Susanne; Simmons, Zachary; van den Berg, Leonard H; Zinman, Lorne; Kupfer, Stuart; Malik, Fady I; Meng, Lisa; Simkins, Tyrell J; Wei, Jenny; Wolff, Andrew A; Rudnicki, Stacy A

Derisking Phase II Clinical Trials in Heart Failure: A Position Paper from JACC: Basic to Translational Science and the Heart Failure Collaboratory

降低心力衰竭 II 期临床试验风险:JACC:基础到转化科学和心力衰竭合作研究室的立场文件

Mann, Douglas L; Felker, G Michael; Unger, Ellis F; Wittes, Janet T; Bozkurt, Biykem; Malik, Fady I; Stockbridge, Norman; Saville, Benjamin R; Fiuzat, Mona; O'Connor, Christopher M; Solomon, Scott D

Characterization and Application of Novel Exercise Recovery Patterns That Reflect Cardiac Performance: A Substudy of the SEQUOIA-HCM Trial

反映心脏功能的新型运动恢复模式的特征分析与应用:SEQUOIA-HCM试验的子研究

Campain, Joseph; Griskowitz, Catharine; Newlands, Chloe; Claggett, Brian L; Kulac, Ian J; McGinnis, Shaina; Giverts, Ilya; Moreno, Fabely; Minasian, Alexandra; Prasad, Cheshta; Rupert, Lillian; Landsteiner, Isabela; Iskenderian, Nick; Coats, Caroline J; Lee, Matthew M Y; Maron, Martin S; Owens, Anjali T; Jacoby, Daniel L; Heitner, Stephen B; Kupfer, Stuart; Malik, Fady I; Wohltman, Amy; Malhotra, Rajeev; Lewis, Gregory D

Cardiac biomarkers and effects of aficamten in obstructive hypertrophic cardiomyopathy: the SEQUOIA-HCM trial

梗阻性肥厚型心肌病患者的心脏生物标志物及阿菲卡明疗效:SEQUOIA-HCM试验

Coats, Caroline J; Masri, Ahmad; Barriales-Villa, Roberto; Abraham, Theodore P; Brinkley, Douglas Marshall; Claggett, Brian L; Hagege, Albert; Hegde, Sheila M; Ho, Carolyn Y; Kulac, Ian J; Lee, Matthew M Y; Maron, Martin S; Olivotto, Iacopo; Owens, Anjali T; Solomon, Scott D; Tfelt-Hansen, Jacob; Watkins, Hugh; Jacoby, Daniel L; Heitner, Stephen B; Kupfer, Stuart; Malik, Fady I; Meng, Lisa; Wohltman, Amy; Januzzi, James L

Effect of Aficamten on Health Status Outcomes in Obstructive Hypertrophic Cardiomyopathy: Results From SEQUOIA-HCM

Aficamten 对梗阻性肥厚型心肌病患者健康状况结局的影响:SEQUOIA-HCM 研究结果

Sherrod, Charles F 4th; Saberi, Sara; Nassif, Michael E; Claggett, Brian L; Coats, Caroline J; Garcia-Pavia, Pablo; Januzzi, James L; Lewis, Gregory D; Ma, Changsheng; Maron, Martin S; Miao, Zi Michael; Olivotto, Iacopo; Veselka, Josef; Butzner, Michael; Jacoby, Daniel L; Heitner, Stephen B; Kupfer, Stuart; Malik, Fady I; Meng, Lisa; Wohltman, Amy; Spertus, John A

Super-relaxed myosins contribute to respiratory muscle hibernation in mechanically ventilated patients

肌球蛋白过度松弛会导致机械通气患者的呼吸肌进入休眠状态。

van den Berg, Marloes; Shi, Zhonghua; Claassen, Wout J; Hooijman, Pleuni; Lewis, Christopher T A; Andersen, Jesper L; van der Pijl, Robbert J; Bogaards, Sylvia J P; Conijn, Stefan; Peters, Eva L; Begthel, Leon P L; Uijterwijk, Bas; Lindqvist, Johan; Langlais, Paul R; Girbes, Armand R J; Stapel, Sandra; Granzier, Henk; Campbell, Kenneth S; Ma, Weikang; Irving, Thomas; Hwee, Darren T; Hartman, James J; Malik, Fady I; Paul, Marinus; Beishuizen, Albertus; Ochala, Julien; Heunks, Leo; Ottenheijm, Coen A C

Aficamten and Cardiopulmonary Exercise Test Performance: A Substudy of the SEQUOIA-HCM Randomized Clinical Trial

Aficamten 与心肺运动试验表现:SEQUOIA-HCM 随机临床试验的子研究

Lee, Matthew M Y; Masri, Ahmad; Nassif, Michael E; Barriales-Villa, Roberto; Abraham, Theodore P; Claggett, Brian L; Coats, Caroline J; Gimeno, Juan Ramón; Kulac, Ian J; Landsteiner, Isabela; Ma, Changsheng; Maron, Martin S; Olivotto, Iacopo; Owens, Anjali T; Solomon, Scott D; Veselka, Josef; Jacoby, Daniel L; Heitner, Stephen B; Kupfer, Stuart; Malik, Fady I; Meng, Lisa; Wohltman, Amy; Lewis, Gregory D

Aficamten is a small-molecule cardiac myosin inhibitor designed to treat hypertrophic cardiomyopathy

Aficamten是一种小分子心肌肌球蛋白抑制剂,旨在治疗肥厚型心肌病。

Hartman, James J; Hwee, Darren T; Robert-Paganin, Julien; Chuang, Chihyuan; Chin, Eva R; Edell, Samantha; Lee, Ken H; Madhvani, Roshni; Paliwal, Preeti; Pernier, Julien; Sarkar, Saswata Sankar; Schaletzky, Julia; Schauer, Kristine; Taheri, Khanha D; Wang, Jingying; Wehri, Eddie; Wu, Yangsong; Houdusse, Anne; Morgan, Bradley P; Malik, Fady I