Safety and early efficacy outcomes for lentiviral fibroblast gene therapy in recessive dystrophic epidermolysis bullosa
慢病毒成纤维细胞基因治疗隐性营养不良型大疱性表皮松解症的安全性和早期疗效结果
期刊:JCI Insight
影响因子:6.3
doi:10.1172/jci.insight.126243
Su M Lwin, Farhatullah Syed, Wei-Li Di, Tendai Kadiyirire, Lu Liu, Alyson Guy, Anastasia Petrova, Alya Abdul-Wahab, Fiona Reid, Rachel Phillips, Maria Elstad, Christos Georgiadis, Sophia Aristodemou, Patricia A Lovell, James R McMillan, John Mee, Snaigune Miskinyte, Matthias Titeux, Linda Ozoemena,