Real-World Safety and Effectiveness of Voretigene Neparvovec: Results up to 2 Years from the Prospective, Registry-Based PERCEIVE Study
Voretigene Neparvovec 的真实世界安全性和有效性:前瞻性、基于注册研究的 PERCEIVE 研究长达 2 年的结果
期刊:Biomolecules
影响因子:4.8
doi:10.3390/biom14010122
Fischer, M Dominik; Simonelli, Francesca; Sahni, Jayashree; Holz, Frank G; Maier, Rainer; Fasser, Christina; Suhner, Andrea; Stiehl, Daniel P; Chen, Bee; Audo, Isabelle; Leroy, Bart P