Degraded sensory coding in a mouse model of Scn2a-related disorder and its rescue by CRISPRa gene activation.
Scn2a相关疾病小鼠模型中的感觉编码退化及其通过CRISPRa基因激活的挽救。
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影响因子:
doi:10.64898/2025.12.13.694145
Vandemark Kaeli, Monday Hannah R, Rodriguez Lucia, Zhao Manya, Lee Meeseo, Ahituv Amit, Satapathy Anwita, Page Nicholas F, An Kelly, Hamada Elizabeth, Ahituv Nadav, Bender Kevin J, Feldman Daniel E