Identification of Ezetimibe and Pranlukast as Pharmacological Chaperones for the Treatment of the Rare Disease Mucopolysaccharidosis Type IVA
鉴定依折麦布和普仑司特作为治疗罕见疾病粘多糖贮积症 IVA 型的药理伴侣
期刊:Journal of Medicinal Chemistry
影响因子:6.8
doi:10.1021/acs.jmedchem.9b00428
Carlos J Alméciga-Diaz, Oscar A Hidalgo, Sergio Olarte-Avellaneda, Alexander Rodríguez-López, Esteban Guzman, Rafael Garzón, Luisa Natalia Pimentel-Vera, María Alejandra Puentes-Tellez, Andrés Felipe Rojas-Rodriguez, Kirill Gorshkov, Rong Li, Wei Zheng
