日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Modulation of the clonal burden in patients with lower-risk myelodysplastic neoplasms treated with imetelstat

伊美替司他治疗低危骨髓增生异常综合征患者的克隆负荷调节

Santini, Valeria; Zeidan, Amer M; Van Eygen, Koen; Fenaux, Pierre; Germing, Ulrich; Madanat, Yazan F; Raza, Azra; Savona, Michael R; Sekeres, Mikkael A; Thépot, Sylvain; Raddi, Marco G; Boyer, Thomas; Sun, Libo; Wan, Ying; Berry, Tymara; Xia, Qi; Huang, Fei; Dougherty, Souria; Navada, Shyamala; Feller, Faye; Komrokji, Rami S; Platzbecker, Uwe

Does stringent cytoreduction improve survival in advanced proliferative chronic myelomonocytic leukemia?

严格的细胞减灭术能否提高晚期增殖性慢性粒单核细胞白血病患者的生存率?

Selimoglu-Buet, Dorothée; Chevret, Sylvie; Santini, Valeria; Thépot, Sylvain; Morabito, Margot; Adès, Lionel; Laplane, Lucie; Giagounidis, Aristoteles; Droin, Nathalie; Lübbert, Michael; Sapena, Rosa; Nimubona, Stanislas; Torregrosa-Diaz, Jose Miguel; Germing, Ulrich; Pelizzari, Anna Maria; Park, Sophie; Jaekel, Nadja; Metzgeroth, Georgia; Onida, Francesco; Paul, Franciane; Patriarca, Andrea; Stamatoullas, Aspasia; Götze, Katharina; Chermat, Fatiha; Platzbecker, Uwe; Fenaux, Pierre; Solary, Eric; Itzykson, Raphael

Association between treatment-emergent cytopenias and clinical responses to imetelstat in lower-risk myelodysplastic syndromes

低危骨髓增生异常综合征患者治疗期间出现的血细胞减少症与伊美替司他临床疗效之间的关联

Zeidan, Amer M; Santini, Valeria; Díez-Campelo, María; Savona, Michael R; Sekeres, Mikkael A; Madanat, Yazan F; Fenaux, Pierre; Raza, Azra; Mittelman, Moshe; Thépot, Sylvain; Buckstein, Rena; Germing, Ulrich; Valcárcel, David; Jonášová, Anna; Shah, Sheetal; Xia, Qi; Sun, Libo; Navada, Shyamala; Berry, Tymara; Platzbecker, Uwe; Komrokji, Rami S

Lupuslike Manifestations in Myelodysplastic Syndromes and Chronic Myelomonocytic Leukemia

骨髓增生异常综合征和慢性粒单核细胞白血病中的狼疮样表现

Chauffier, Jeanne; Jachiet, Vincent; Battistella, Maxime; Romero, Pierre; Fenaux, Pierre; Zakine, Eve; Zhao, Lin Pierre; Mahévas, Thibault; Bouaziz, Jean-David; Hadjadj, Jerome; Amoura, Zahir; Mathian, Alexis; Breillat, Paul; Hirsch, Pierre; Bourguiba, Rim; De Voeght, Adrien; Grobost, Vincent; Begon, Edouard; Jandus, Peter; Brenaut, Emilie; Laumondais, Victoire; Fain, Olivier; Moguelet, Philippe; Mekinian, Arsene; Chasset, François

American College of Rheumatology Guidance Statement for Diagnosis and Management of VEXAS Developed by the International VEXAS Working Group Expert Panel

美国风湿病学会关于VEXAS诊断和治疗的指导声明,由国际VEXAS工作组专家组制定

Mekinian, Arsene; Georgin-Lavialle, Sophie; Ferrada, Marcela A; Savic, Sinisa; Koster, Matthew J; Kosmider, Olivier; Comont, Thibault; Heiblig, Mael; Arostegui, Juan I; Bosco, Annmarie; Bourguiba, Rim; Calvo, Katherine R; Cargo, Catherine; Cattaneo, Chiara; Chasset, François; Coelho, Henrique; Campochiaro, Corrado; Crisafulli, Francesca; Ducharme-Benard, Stephanie; Faria, Raquel; Franceschini, Franco; Frassi, Micol; Groarke, Emma M; Gurnari, Carmelo; Hakobyan, Yervand; Jamilloux, Yvan; Jurcut, Ciprian; Kirino, Yohei; Kulasekararaj, Austin; Kunimoto, Hiroyoshi; Madigan, Lauren M; Mann, Heřman F; Marvisi, Chiara; Milchert, Marcin; Morais, Sara; Sockel, Katja; Muratore, Francesco; Nakajima, Hideaki; Patnaik, Mrinal M; Regadas, Luísa; Robin, Marie; Rutgers, Abraham; Salvarani, Carlo; Sammel, Anthony M; Seebach, Joerg; Sujobert, Pierre; Tomelleri, Alessandro; Urbanski, Geoffrey; Vandergheynst, Frédéric; Vieira, Romana; Viswanatha, David S; Więsik-Szewczyk, Ewa; Diral, Elisa; Terrier, Benjamin; Patel, Bhavisha A; Fenaux, Pierre; Grayson, Peter C; Beck, David B

Transplantation in patients with lower-risk MDS: a prospective phase 2 trial based on donor availability

低危MDS患者的移植:一项基于供体可用性的前瞻性II期试验

Sébert, Marie; Thepot, Sylvain; Cluzeau, Thomas; Duployez, Nicolas; Lefèbvre, Thibaud; Chaffaut, Cendrine; Orvain, Corentin; Loschi, Michael; Peterlin, Pierre; Chevallier, Patrice; D'Aveni, Maud; Rubio, Marie Thérèse; Rauzy, Odile; Huynh, Anne; Charbonnier, Amandine; Sapena, Rosa; Chermat, Fatiha; Ceballos, Patrice; Fossard, Gaelle; Nguyen, Stéphanie; Park, Sophie; Adès, Lionel; Peffault de Latour, Régis; Preudhomme, Claude; Fenaux, Pierre; Chevret, Sylvie; Robin, Marie

Clinical outcomes and safety in patients with lower-risk myelodysplastic syndromes treated with imetelstat: Substudy of the phase 3 IMerge trial

伊美替司他治疗低危骨髓增生异常综合征患者的临床结果和安全性:3期IMerge试验的子研究

Komrokji, Rami S; Santini, Valeria; Platzbecker, Uwe; Van Eygen, Koen; Díez-Campelo, María; de Paz, Raquel; Santillana, Guillermo Sanz; Thépot, Sylvain; Kaźmierczak, Maciej; Oliva, Esther Natalie; Sekeres, Mikkael A; Fenaux, Pierre; Madanat, Yazan F; Savona, Michael R; Riggs, Jennifer; Shah, Sheetal; Lennox, Ashley L; Xia, Qi; Sun, Libo; Berry, Tymara; Zeidan, Amer M

European Reference Networks - a flagship activity of the EU in the field of rare and complex diseases: from 2017 to 2025

欧洲参考网络——欧盟在罕见病和复杂疾病领域的一项旗舰活动:2017年至2025年

Graessner, Holm; Ripp, Sophie; Pereira, Alberto M; Schaefer, Franz; Mathijssen, Irene; Blay, Jean-Yves; Mulders, Peter F A; Evangelista, Teresinha; Ligtenberg, Marjolijn J L; Wilde, Arthur A M; Ladenstein, Ruth; Lohse, Ansgar W; Mosca, Marta; Swart, Joost Frans; Hernández, Francisco; Fenaux, Pierre; Dollfus, Hélène; Verloes, Alain; Wagner, Thomas; Bodemer, Christine; Wijnen, Rene; Scarpa, Maurizio; Jondeau, Guillaume; Tumienė, Birutė; Gallina, Sandra; Arzimanoglou, Alexis; Sangiorgi, Luca

Characterization and Clinical Implications of p53 Dysfunction in Patients With Myelodysplastic Syndromes

骨髓增生异常综合征患者p53功能障碍的特征及临床意义

Zampini, Matteo; Riva, Elena; Lanino, Luca; Sauta, Elisabetta; Antunes Dos Reis, Rita; Ejarque, Rosa Maria Andres; Maggioni, Giulia; Termanini, Alberto; Merlotti, Alessandra; Campagna, Alessia; Dall'Olio, Lorenzo; Kulasekararaj, Austin; Calvi, Michela; Di Vito, Clara; Bonometti, Arturo; Rahal, Daoud; Croci, Giorgio; Boveri, Emanuela; Gianelli, Umberto; Ponzoni, Maurilio; Caselli, Rossella; Albertazzi, Serena; Todisco, Gabriele; Ubezio, Marta; Crisafulli, Laura; Frigo, Alessandro; Lugli, Enrico; Mosca, Ettore; Acha, Pamela; Ghisletti, Serena; Nicassio, Francesco; Santoro, Armando; Diez-Campelo, Maria; Solé, Francesc; Ades, Lionel; Platzbecker, Uwe; Santini, Valeria; Fenaux, Pierre; Haferlach, Torsten; Sallman, David; Garcia-Manero, Guillermo; Mavilio, Domenico; Remondini, Daniel; Castellani, Gastone; D'Amico, Saverio; Zeidan, Amer M; Komrokji, Rami; Kordasti, Shahram; Ficara, Francesca; Della Porta, Matteo Giovanni

Olutasidenib for mutated IDH1 acute myeloid leukemia: final five-year results from the phase 2 pivotal cohort

Olutasidenib治疗IDH1突变型急性髓系白血病:II期关键队列的五年最终结果

Cortes, Jorge; Curti, Antonio; Fenaux, Pierre; Jonas, Brian A; Krauter, Jürgen; Montesinos, Pau; Récher, Christian; Taussig, David C; Wang, Eunice S; Watts, Justin; Wei, Andrew; Yee, Karen Wl; Tian, Hua; Sheppard, Aaron; Marzac, Christophe; de Botton, Stephane