A phase 4, open-label, multicenter study of the safety and efficacy of agalsidase beta in Chinese patients with Fabry disease
一项评估阿加糖酶β治疗中国法布里病患者的安全性和有效性的4期、开放标签、多中心研究
期刊:Orphanet Journal of Rare Diseases
影响因子:3.5
doi:10.1186/s13023-025-03950-7
Ren, Hong; Zhang, Wei; Ouyang, Yan; Guo, Junhong; Xu, Hong; Ma, Jie; Luo, Xiaoping; Pan, Xiaoxia; Yuan, Yun; Zhang, Wei; Shen, Qian; Li, Bin; Feng, Qiqi; Liu, Shi; Chen, Nan