Durable transgene expression and efficient re-administration after rAAV2.5T-mediated fCFTRΔR gene delivery to adult ferret lungs
rAAV2.5T介导的fCFTRΔR基因递送至成年雪貂肺部后,转基因表达持久且可有效重复给药
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2024.101244
Tang, Yinghua; Ebadi, Mehrnoosh; Lei, Junying; Feng, Zehua; Fakhari, Shahab; Wu, Peipei; Smith, Mark D; Limberis, Maria P; Kolbeck, Roland; Excoffon, Katherine J; Yan, Ziying; Engelhardt, John F