Preclinical efficacy and safety of AAVrh10-based plakophilin-2 gene therapy (LX2020) as a treatment for arrhythmogenic cardiomyopathy.
基于 AAVrh10 的 plakophilin-2 基因疗法 (LX2020) 治疗致心律失常性心肌病的临床前疗效和安全性
期刊:npj Regenerative Medicine
影响因子:6.5
doi:10.1038/s41536-025-00401-6
Zhang Jing, Gutierrez-Lara Erika Joana, Do Aryanne, Nguyen Lena, Nair Anju, Selvan Nithya, Fenn Tim, Adler Eric, Khanna Richie, Sheikh Farah
