日期 影响因子
日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:
–

Retinal gene therapy for Stargardt disease with dual AAV intein vectors is both safe and effective in large animal models.

使用双AAV内含子载体的视网膜基因疗法治疗Stargardt病在大动物模型中安全有效

期刊:Science Advances
影响因子:12.5
doi:10.1126/sciadv.adt9354
Ferla Rita, Pugni Eugenio, Lupo Mariangela, Tiberi Paola, Fioretto Federica, Perota Andrea, Duchi Roberto, Lagutina Irina, Gesualdo Carlo, Rossi Settimio, Ventrella Domenico, Elmi Alberto, McClinton Benjamin, Toomes Carmel, Xu Tongzhou, Molday Robert S, Surace Enrico M, Simonelli Francesca, Bacci Maria L, Galli Cesare, Memon Muhammad A, Shams Naveed, Auricchio Alberto, Trapani Ivana
发表日期：2025
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Low incidence of hepatocellular carcinoma in mice and cats treated with systemic adeno-associated viral vectors.

用全身性腺相关病毒载体治疗的小鼠和猫中肝细胞癌的发生率较低

期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2020.11.015
Ferla Rita, Alliegro Marialuisa, Dell'Anno Margherita, Nusco Edoardo, Cullen John M, Smith Stephanie N, Wolfsberg Tyra G, O'Donnell Patricia, Wang Ping, Nguyen Anh-Dao, Chandler Randy J, Chen Zelin, Burgess Shawn M, Vite Charles H, Haskins Mark E, Venditti Charles P, Auricchio Alberto
细胞生物学
Viral
发表日期：2021
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Gene therapy for mucopolysaccharidosis type VI is effective in cats without pre-existing immunity to AAV8

针对粘多糖贮积症VI型的基因疗法对未预先对AAV8产生免疫力的猫有效。

期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2012.179
Ferla, Rita; O'Malley, Thomas; Calcedo, Roberto; O'Donnell, Patricia; Wang, Ping; Cotugno, Gabriella; Claudiani, Pamela; Wilson, James M; Haskins, Mark; Auricchio, Alberto
免疫/内分泌
发表日期：2013
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