日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Patient-reported outcomes in patients with paroxysmal nocturnal hemoglobinuria treated with crovalimab and approved C5 inhibitors in the phase III COMMODORE 2 and 1 studies

在 III 期 COMMODORE 2 和 1 研究中,接受 crovalimab 和已批准的 C5 抑制剂治疗的阵发性睡眠性血红蛋白尿患者的患者报告结局

Panse, Jens; Han, Bing; Cermak, Jaroslav; Gonzalez Fernandez, Fernando Ataulfo; Gotoh, Akihiko; Kulasekararaj, Austin G; Kyselova, Olena; Sahin, Fahri; Scheinberg, Phillip; Schrezenmeier, Hubert; Straetmans, Nicole; Ueda, Yasutaka; Chang, Alice C; Gentile, Brittany; Stefani, Jennifer; Uguen, Marianne; Röth, Alexander

Mutations in the RACGAP1 gene cause autosomal recessive congenital dyserythropoietic anemia type III

RACGAP1基因突变导致常染色体隐性遗传性先天性红细胞生成障碍性贫血III型

Hernández, Gonzalo; Romero-Cortadellas, Lídia; Ferrer-Cortès, Xènia; Venturi, Veronica; Dessy-Rodriguez, Mercedes; Olivella, Mireia; Husami, Ammar; De Soto, Concepción Pérez; Morales-Camacho, Rosario M; Villegas, Ana; González-Fernández, Fernando-Ataulfo; Morado, Marta; Kalfa, Theodosia A; Quintana-Bustamante, Oscar; Pérez-Montero, Santiago; Tornador, Cristian; Segovia, Jose-Carlos; Sánchez, Mayka