Gene transfer to the CNS is efficacious in immune-primed mice harboring physiologically relevant titers of anti-AAV antibodies
在体内含有生理相关滴度抗AAV抗体的免疫预激活小鼠中,基因转移到中枢神经系统是有效的。
期刊:Molecular Therapy
影响因子:12
doi:10.1038/mt.2012.114
Treleaven, Christopher M; Tamsett, Thomas J; Bu, Jie; Fidler, Jonathan A; Sardi, S Pablo; Hurlbut, Gregory D; Woodworth, Lisa A; Cheng, Seng H; Passini, Marco A; Shihabuddin, Lamya S; Dodge, James C