Design of efficacious somatic cell genome editing strategies for recessive and polygenic diseases
针对隐性和多基因疾病的有效体细胞基因组编辑策略的设计
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-020-20065-8
Jared Carlson-Stevermer, Amritava Das, Amr A Abdeen, David Fiflis, Benjamin I Grindel, Shivani Saxena, Tugce Akcan, Tausif Alam, Heidi Kletzien, Lucille Kohlenberg, Madelyn Goedland, Micah J Dombroe, Krishanu Saha