日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Confirmed efficacy of etoposide and dexamethasone in HLH treatment: long-term results of the cooperative HLH-2004 study

证实依托泊苷和地塞米松治疗HLH的疗效:HLH-2004合作研究的长期结果

Bergsten, Elisabet; Horne, AnnaCarin; Aricó, Maurizio; Astigarraga, Itziar; Egeler, R Maarten; Filipovich, Alexandra H; Ishii, Eiichi; Janka, Gritta; Ladisch, Stephan; Lehmberg, Kai; McClain, Kenneth L; Minkov, Milen; Montgomery, Scott; Nanduri, Vasanta; Rosso, Diego; Henter, Jan-Inge

Haematopoietic stem cell transplantation for refractory Langerhans cell histiocytosis: outcome by intensity of conditioning

造血干细胞移植治疗难治性朗格汉斯细胞组织细胞增生症:预处理强度与疗效的关系

Veys, Paul A; Nanduri, Vasanta; Baker, K Scott; He, Wensheng; Bandini, Giuseppe; Biondi, Andrea; Dalissier, Arnaud; Davis, Jeffrey H; Eames, Gretchen M; Egeler, R Maarten; Filipovich, Alexandra H; Fischer, Alain; Jürgens, Herbert; Krance, Robert; Lanino, Edoardo; Leung, Wing H; Matthes, Susanne; Michel, Gérard; Orchard, Paul J; Pieczonka, Anna; Ringdén, Olle; Schlegel, Paul G; Sirvent, Anne; Vettenranta, Kim; Eapen, Mary

Transplantation outcomes for severe combined immunodeficiency, 2000-2009

2000-2009年重症联合免疫缺陷患者的移植结果

Pai, Sung-Yun; Logan, Brent R; Griffith, Linda M; Buckley, Rebecca H; Parrott, Roberta E; Dvorak, Christopher C; Kapoor, Neena; Hanson, Imelda C; Filipovich, Alexandra H; Jyonouchi, Soma; Sullivan, Kathleen E; Small, Trudy N; Burroughs, Lauri; Skoda-Smith, Suzanne; Haight, Ann E; Grizzle, Audrey; Pulsipher, Michael A; Chan, Ka Wah; Fuleihan, Ramsay L; Haddad, Elie; Loechelt, Brett; Aquino, Victor M; Gillio, Alfred; Davis, Jeffrey; Knutsen, Alan; Smith, Angela R; Moore, Theodore B; Schroeder, Marlis L; Goldman, Frederick D; Connelly, James A; Porteus, Matthew H; Xiang, Qun; Shearer, William T; Fleisher, Thomas A; Kohn, Donald B; Puck, Jennifer M; Notarangelo, Luigi D; Cowan, Morton J; O'Reilly, Richard J

A modified γ-retrovirus vector for X-linked severe combined immunodeficiency

用于治疗X连锁重症联合免疫缺陷的改良型γ逆转录病毒载体

Hacein-Bey-Abina, Salima; Pai, Sung-Yun; Gaspar, H Bobby; Armant, Myriam; Berry, Charles C; Blanche, Stephane; Bleesing, Jack; Blondeau, Johanna; de Boer, Helen; Buckland, Karen F; Caccavelli, Laure; Cros, Guilhem; De Oliveira, Satiro; Fernández, Karen S; Guo, Dongjing; Harris, Chad E; Hopkins, Gregory; Lehmann, Leslie E; Lim, Annick; London, Wendy B; van der Loo, Johannes C M; Malani, Nirav; Male, Frances; Malik, Punam; Marinovic, M Angélica; McNicol, Anne-Marie; Moshous, Despina; Neven, Benedicte; Oleastro, Matías; Picard, Capucine; Ritz, Jerome; Rivat, Christine; Schambach, Axel; Shaw, Kit L; Sherman, Eric A; Silberstein, Leslie E; Six, Emmanuelle; Touzot, Fabien; Tsytsykova, Alla; Xu-Bayford, Jinhua; Baum, Christopher; Bushman, Frederic D; Fischer, Alain; Kohn, Donald B; Filipovich, Alexandra H; Notarangelo, Luigi D; Cavazzana, Marina; Williams, David A; Thrasher, Adrian J

Synergistic defects of different molecules in the cytotoxic pathway lead to clinical familial hemophagocytic lymphohistiocytosis

细胞毒性通路中不同分子的协同缺陷会导致临床上的家族性噬血细胞性淋巴组织细胞增生症。

Zhang, Kejian; Chandrakasan, Shanmuganathan; Chapman, Heather; Valencia, C Alexander; Husami, Ammar; Kissell, Diane; Johnson, Judith A; Filipovich, Alexandra H

Recommendations for live viral and bacterial vaccines in immunodeficient patients and their close contacts

关于免疫缺陷患者及其密切接触者接种活病毒和细菌疫苗的建议

Shearer, William T; Fleisher, Thomas A; Buckley, Rebecca H; Ballas, Zuhair; Ballow, Mark; Blaese, R Michael; Bonilla, Francisco A; Conley, Mary Ellen; Cunningham-Rundles, Charlotte; Filipovich, Alexandra H; Fuleihan, Ramsay; Gelfand, Erwin W; Hernandez-Trujillo, Vivian; Holland, Steven M; Hong, Richard; Lederman, Howard M; Malech, Harry L; Miles, Stephen; Notarangelo, Luigi D; Ochs, Hans D; Orange, Jordan S; Puck, Jennifer M; Routes, John M; Stiehm, E Richard; Sullivan, Kathleen; Torgerson, Troy; Winkelstein, Jerry

Primary Immune Deficiency Treatment Consortium (PIDTC) report

原发性免疫缺陷治疗联盟(PIDTC)报告

Griffith, Linda M; Cowan, Morton J; Notarangelo, Luigi D; Kohn, Donald B; Puck, Jennifer M; Pai, Sung-Yun; Ballard, Barbara; Bauer, Sarah C; Bleesing, Jack J H; Boyle, Marcia; Brower, Amy; Buckley, Rebecca H; van der Burg, Mirjam; Burroughs, Lauri M; Candotti, Fabio; Cant, Andrew J; Chatila, Talal; Cunningham-Rundles, Charlotte; Dinauer, Mary C; Dvorak, Christopher C; Filipovich, Alexandra H; Fleisher, Thomas A; Bobby Gaspar, Hubert; Gungor, Tayfun; Haddad, Elie; Hovermale, Emily; Huang, Faith; Hurley, Alan; Hurley, Mary; Iyengar, Sumathi; Kang, Elizabeth M; Logan, Brent R; Long-Boyle, Janel R; Malech, Harry L; McGhee, Sean A; Modell, Fred; Modell, Vicki; Ochs, Hans D; O'Reilly, Richard J; Parkman, Robertson; Rawlings, David J; Routes, John M; Shearer, William T; Small, Trudy N; Smith, Heather; Sullivan, Kathleen E; Szabolcs, Paul; Thrasher, Adrian; Torgerson, Troy R; Veys, Paul; Weinberg, Kenneth; Zuniga-Pflucker, Juan Carlos

Whole-exome sequencing reveals overlap between macrophage activation syndrome in systemic juvenile idiopathic arthritis and familial hemophagocytic lymphohistiocytosis

全外显子组测序揭示了系统性幼年特发性关节炎中的巨噬细胞活化综合征与家族性噬血细胞性淋巴组织细胞增生症之间的重叠。

Kaufman, Kenneth M; Linghu, Bolan; Szustakowski, Joseph D; Husami, Ammar; Yang, Fan; Zhang, Kejian; Filipovich, Alexandra H; Fall, Ndate; Harley, John B; Nirmala, N R; Grom, Alexei A

The successful use of alemtuzumab for treatment of steroid-refractory acute graft-versus-host disease in pediatric patients

阿仑单抗成功用于治疗儿童类固醇难治性急性移植物抗宿主病

Khandelwal, Pooja; Lawrence, Julia; Filipovich, Alexandra H; Davies, Stella M; Bleesing, Jacob J; Jordan, Michael B; Mehta, Parinda; Jodele, Sonata; Grimley, Michael S; Kumar, Ashish; Myers, Kasiani; Marsh, Rebecca A

Salvage therapy of refractory hemophagocytic lymphohistiocytosis with alemtuzumab

阿仑单抗用于难治性噬血细胞性淋巴组织细胞增生症的挽救治疗

Marsh, Rebecca A; Allen, Carl E; McClain, Kenneth L; Weinstein, Joanna L; Kanter, Julie; Skiles, Jodi; Lee, Nadine D; Khan, Shakila P; Lawrence, Julia; Mo, Jun Q; Bleesing, Jack J; Filipovich, Alexandra H; Jordan, Michael B