Treatment with THI, an inhibitor of sphingosine-1-phosphate lyase, modulates glycosphingolipid metabolism and results therapeutically effective in experimental models of Huntington's disease
使用 THI(一种鞘氨醇-1-磷酸裂解酶抑制剂)进行治疗,可以调节糖鞘脂代谢,对亨廷顿氏病的实验模型具有治疗效果
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2022.09.004
Giuseppe Pepe, Luca Capocci, Federico Marracino, Natalia Realini, Paola Lenzi, Katiuscia Martinello, Tiziana Francesca Bovier, Terry Jo Bichell, Pamela Scarselli, Clotilde Di Cicco, Aaron B Bowman, Filomena A Digilio, Sergio Fucile, Francesco Fornai, Andrea Armirotti, Rosanna Parlato, Alba Di Pardo,