日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Durable HTT silencing using non-evolved dCas9 epigenome editors in patient-derived cells.

利用非进化型 dCas9 表观基因组编辑器在患者来源细胞中实现持久的 HTT 沉默

Waldo Jennifer J, Halmai Julian A N M, Singh Ankita, Gonzalez Casiana E, Chen Yi-An, Carthen Shaylyn A, Nolta Jan A, Fink Kyle D

A de novo missense mutation in PPP2R5D alters dopamine pathways and morphology of iPSC-derived midbrain neurons.

PPP2R5D 中的新生错义突变改变了 iPSC 衍生的中脑神经元的多巴胺通路和形态

Carter Jasmine L, Halmai Julian A N M, Waldo Jennifer J, Vij Paula A, Anguiano Maribel, Villegas Isaac J, Du Yu Xin, Nolta Jan, Fink Kyle D

Long-Term Engraftment of Cryopreserved Human Neurons for In Vivo Disease Modeling in Neurodegenerative Disease.

冷冻保存的人类神经元长期移植用于神经退行性疾病的体内疾病建模

Marmion David J, Deng Peter, Hiller Benjamin M, Lewis Rachel L, Harms Lisa J, Cameron David L, Nolta Jan A, Kordower Jeffrey H, Fink Kyle D, Wakeman Dustin R

Assigning Targetable Molecular Pathways to Transdiagnostic Subgroups Across Autism and Related Neurodevelopmental Disorders

为自闭症及相关神经发育障碍的跨诊断亚组分配可靶向分子通路

Ellegood, Jacob; Beauchamp, Antoine; Yee, Yohan; Devenyi, Gabe; Ziolkowski, Justine; Qiu, Lily; Askalan, Rand; Ayub, Muhammad; Suetterlin, Philipp; Donovan, Alex; Basson, M Albert; Quesnel, Katherine M; Berube, Nathalie G; Woo, Taeseon; Beversdorf, David; Bjornsson, Hans; Blakely, Randy; Crawley, Jacqueline; Crosbie, Jennifer; Orr, Brian O; Davis, Graeme W; Genestine, Matthew; DiCicco-Bloom, Emanuel; Egan, Sean; Fink, Kyle D; Asbury, Sarah; Lai, Jonathan; Rilett, Kelly; Foster, Jane A; Vincent, John B; Frankland, Paul; Georgiades, Stelios; Penagarikano, Olga; Geschwind, Daniel; Giger, Roman J; Markx, Sander; Gogos, Joseph; Golzio, Christelle; Pagani, Marco; Gozzi, Alessandro; Pacey, Laura K; Hampson, David; Huang, Tzyy-Nan; Yen, Tzu-Li; Hsueh, Yi-Ping; Iaboni, Alana; Amar, Megha; Iakoucheva, Lilia M; Jones, Jessica K; Kelly, Elizabeth; Kieffer, Brigette; Bae, Mihyun; Jung, Hwajin; Kim, Hyosang; Park, Haram; Roh, Junye Daniel; Kim, Eunjoon; Konopka, Genevieve; Laliberte, Christine; Lefebvre, Julie L; Eagleson, Kathie; Levitt, Pat; Bach, Aurea Martins; Cunningham, Thomas J; Fisher, Elizabeth; Miller, Karla; Mills, Alea; Muotri, Alyson; Nicolson, Rob; Noakes, Leigh Spencer; Nieman, Brian J; Canales, Cesar P; Nord, Alex S; Nutter, Lauryl Mj; Tam, Elaine; Osborne, Lucy R; Clipperton-Allen, Amy; Page, Damon; Babineau, Brooke; Palmer, Theo D; Yan, Keqin; Picketts, David; Xia, Qiangqiang; Powell, Craig M; Raznahan, Armin; Robins, Diane M; Rumbaugh, Gavin; Sengar, Ameet S; Salter, Michael William; Schachar, Russell James; D'Abate, Lia; Bradley, Clarissa A; Scherer, Stephen W; Copping, Nycole W; Petkova, Stela P; Silverman, Jill L; Singh, Karun Kar; Kim, Nam-Shik; Yoon, Ki-Jun Kar; Ming, Guo-Li; Song, Hongjun; Spring, Shoshana; Nakatani, Jin; Nakai, Nobuhiro; Nomura, J; Takumi, Toru; Taylor, Margot; Tsai, Peter; Bruce, Matthew; Jones, Karen L; Van de Water, Judy; Van Eede, Matthijs C; Kerr, Travis M; Muller, Christopher L; VanderWeele, Jeremy Veenstra; Vandewouw, Marlee; Weksberg, Rosanna; Wevrick, Rachel; Belinson, Haim; Wynshaw-Boris, Anthony; Zarbalis, Konstantinos; Trost, Brett; Mars, Rogier B; Chakravarty, Mallar; Kushki, Azadek; Anagnostou, Evdokia; Lerch, Jason P

Epigenetic editing for autosomal dominant neurological disorders

表观遗传编辑在常染色体显性神经系统疾病中的应用

Waldo, Jennifer J; Halmai, Julian A N M; Fink, Kyle D

Polyamine Metabolites as Biomarkers in Head and Neck Cancer Biofluids

多胺代谢物作为头颈癌生物体液中的生物标志物

DeFelice, Brian C; Fiehn, Oliver; Belafsky, Peter; Ditterich, Constanze; Moore, Michael; Abouyared, Marianne; Beliveau, Angela M; Farwell, D Gregory; Bewley, Arnaud F; Clayton, Shannon M; Archard, Joehleen A; Pavlic, Jordan; Rao, Shyam; Kuhn, Maggie; Deng, Peter; Halmai, Julian; Fink, Kyle D; Birkeland, Andrew C; Anderson, Johnathon D

Emerging Gene and Small Molecule Therapies for the Neurodevelopmental Disorder Angelman Syndrome

针对神经发育障碍安格曼综合征的新兴基因和小分子疗法

Copping, Nycole A; McTighe, Stephanie M; Fink, Kyle D; Silverman, Jill L

Cell-Based Delivery Approaches for DNA-Binding Domains to the Central Nervous System

基于细胞的DNA结合域向中枢神经系统递送方法

Deng, Peter; Halmai, Julian; Waldo, Jennifer J; Fink, Kyle D

The iNs and Outs of Direct Reprogramming to Induced Neurons

直接重编程诱导神经元的利弊

Carter, Jasmine L; Halmai, Julian A N M; Fink, Kyle D

Engineered BDNF producing cells as a potential treatment for neurologic disease

工程改造的BDNF产生细胞作为神经系统疾病的潜在治疗方法

Deng, Peter; Anderson, Johnathon D; Yu, Abigail S; Annett, Geralyn; Fink, Kyle D; Nolta, Jan A