日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

High-dose nusinersen for spinal muscular atrophy: a phase 3 randomized trial

高剂量诺西那生治疗脊髓性肌萎缩症:一项3期随机试验

Finkel, Richard S; Crawford, Thomas O; Mercuri, Eugenio; Sumner, Charlotte J; Garcia Romero, Maria Del Mar; Day, John W; Montes, Jacqueline; Sun, Peng; Tichler, Ben; Paradis, Angela D; Boesch, Emily; Inra, Jennifer; Littauer, Ross; Sohn, Jihee; Monine, Michael; Gambino, Giulia; Foster, Richard; Farewell, Raechel; Fradette, Stephanie

Intrathecal onasemnogene abeparvovec in treatment-naive patients with spinal muscular atrophy: a phase 3, randomized controlled trial

鞘内注射onasemnogene abeparvovec治疗初治脊髓性肌萎缩症患者:一项3期随机对照试验

Proud, Crystal M; Vũ, Dũng Chí; Wilmshurst, Jo M; Sanmaneechai, Oranee; Gulati, Sheffali; Xiong, Hui; Moreno, Hugo C; Tay, Stacey Kiat Hong; Thong, Meow-Keong; Born, Alfred Peter; Banzzatto Ortega, Adriana; Jong, Yuh-Jyh; Al-Muhaizea, Mohammad A; Lee, Anna W; Visootsak, Jeannie; Tauscher-Wisniewski, Sitra; Alecu, Iulian; Parlikar, Rutvick; Finkel, Richard S

Fueling the fire: metabolic dysfunction and senescence as drivers of lung aging and disease

火上浇油:代谢功能障碍和衰老是肺部衰老和疾病的驱动因素

Kliment, Corrine R; Gurkar, Aditi U; Cárdenes, Nayra; Ramonell, Richard P; Finkel, Toren; Königshoff, Melanie

Suppression of interferon signaling via small-molecule modulation of TFAM.

通过小分子调节 TFAM 来抑制干扰素信号传导。

Sideris Dionisia, Lee Husan, Olson Lyndsay, Nallaparaju Kalyan, Okuyama Keiichiro, Ciavarri Jeffrey, Lafyatis Robert, Larsen Mads, Lin Bo, Alfaras Irene, Kennerdell Jason, Finkel Toren, Liu Yuan, Chen Bill, Lyu Lin

BRAF and MEK inhibition beyond dabrafenib-trametinib in advanced thyroid cancer: a real-world case series

晚期甲状腺癌中,除达拉非尼-曲美替尼外,BRAF和MEK抑制剂的疗效:一项真实世界病例系列研究

Yamin, Tzahi; Cohen, Oded; Robenshtok, Eyal; Izkhakov, Elena; Miodovnik, Mor; Gutfeld, Orit; Leshem, Yasmin; Meirovitz, Roman; Warshavsky, Anton; Muhanna, Nidal; Finkel, Inbar

Evaluation of statistical differential analysis methods for identification of senescent cells using single-cell transcriptomics

利用单细胞转录组学评估统计差异分析方法在衰老细胞鉴定中的应用

Li, Dongmei; Liu, Pinxin; Rahman, Irfan; Zand, Martin; Pryhuber, Gloria; Dye, Timothy; Goniewicz, Maciej; Gurkar, Aditi Uday; Königshoff, Melanie; Eickelberg, Oliver; Mora, Ana; Rojas, Mauricio; Ma, Qin; Lugo-Martinez, Jose; Bar-Joseph, Ziv; Lanna, Serafina; Finkel, Toren; Xie, Zidian

Nonlinear decline in the association between birth weight and cognitive ability from infancy to midlife in a community sample of twins

一项针对社区双胞胎样本的研究发现,从婴儿期到中年,出生体重与认知能力之间的关联呈非线性下降趋势。

Bell, Sophie A; Womack, Sean R; Kam, Alyssa; Gonenne, Molly; Beam, Christopher R; Giangrande, Evan J; Finkel, Deborah; Turkheimer, Eric; Davis, Deborah W

Moderating effects of educational inequality on education polygenic scores, attained education and dementia-risk relationships

教育不平等对教育多基因评分、受教育程度和痴呆风险关系的影响

Finch, Brian Karl; Nimmagadda, Sneha; Finkel, Deborah; Gatz, Margaret; Reynolds, Chandra A; Nygaard, Marianne; Catts, Vibeke; Thalamuthu, Anbu; Sachdev, Perminder; Ericsson, Malin; Karlsson, Ida; Thorvaldsson, Valgeir; Hassing, Linda

A Novel CEST-Based Approach for Reliably Assessing Skeletal Muscle Oxidative Phosphorylation: OXCEST

一种基于CEST的新型可靠评估骨骼肌氧化磷酸化的方法:OXCEST

Burman, Ritambhar; Pang, Yuxi; Bag, Asim; Finkel, Richard S; Ness, Kirsten K; Bagga, Puneet

Relating consequential falls to individual and combinations of prescription medication use in Swedish older adults

瑞典老年人跌倒事件与处方药的个体及组合使用之间的关系

Peterson, Daniel S; Johansson, Linda; Westerlind, Bjorn; Lopes de Oliveira, Thais; Finkel, Deborah