ENPP1 enzyme replacement therapy improves ectopic calcification but does not rescue skeletal phenotype in a mouse model for craniometaphyseal dysplasia.
ENPP1 酶替代疗法可改善异位钙化,但不能挽救颅骨干骺端发育不良小鼠模型的骨骼表型
期刊:JBMR Plus
影响因子:2.4
doi:10.1093/jbmrpl/ziae103
Reichenberger Ernst J, O'Brien Kevin, Hatori Ayano, Carpenter Thomas O, van de Wetering Koen, Flaman Lisa, Howe Jennifer, Ortiz Daniel, Sabbagh Yves, Chen I-Ping