Preclinical quality, safety, and efficacy of a CGMP iPSC-derived myogenic progenitor product for the treatment of muscular dystrophies.
用于治疗肌营养不良症的 CGMP iPSC 衍生肌源性祖细胞产品的临床前质量、安全性和有效性
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.07.007
Azzag Karim, Magli Alessandro, Kiley James, Sumstad Darin, Kadidlo Diane, Crist Sarah B, Norris Beverly, Ahlquist Aaron, Hocum Stone Laura L, Everett John, Shappa Faustich Jill, Seelig Davis, Rangarajan Parthasarathy, Kim Hyunkee, Flory Craig, Bushman Frederic, Ramachandran Sabarinathan, Kang Peter B, Schumacher Robert J, Wagner John E, Kyba Michael, Graham Melanie L, McKenna David H, Perlingeiro Rita C R
