日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Directed evolution of liver-detargeted AAV vectors for systemic gene delivery to skeletal muscle and heart

定向进化肝脏去靶向AAV载体,用于将基因系统性递送至骨骼肌和心脏

Firnberg, Elad; Tejada, Sigmund K S; Yost, Samantha A; Giles, April R; Choi, Heonhwa; Foltz, Steven J; Qian, Randolph; Smith, Jared B; Heithoff, Benjamin; Elliott, Kirk; David Hou, Chun-Feng; Bernstein, Ashley D; Karumuthil-Melethil, Subha; Chen, Victor Shugui; Mayer, Ayda; Mercer, Andrew C; Kaelber, Jason T; Liu, Ye; Danos, Olivier

Enhanced therapeutic potential of a microdystrophin with an extended C-terminal domain.

具有延长的 C 端结构域的微型肌营养不良蛋白具有增强的治疗潜力。

Foltz Steven J, Qian Randolph, Yang Jason, Elliott Kirk, Heithoff Benjamin P, Jasick Hannah, Smith Jared B, Karumuthil-Melethil Subha, Qiao Chunping, Liu Ye, Danos Olivier

Abnormal Skeletal Muscle Regeneration plus Mild Alterations in Mature Fiber Type Specification in Fktn-Deficient Dystroglycanopathy Muscular Dystrophy Mice.

Fktn 缺乏型肌营养不良蛋白病小鼠出现异常骨骼肌再生和成熟纤维类型分化轻微改变

Foltz Steven J, Modi Jill N, Melick Garrett A, Abousaud Marin I, Luan Junna, Fortunato Marisa J, Beedle Aaron M